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GeneE
10 sources retrieved Β· Most recent: April 2026 Β· Index updated 14 days ago
β“˜GeneE is for informational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment.
COX20
cytochrome c oxidase assembly factor COX20
Chromosome 1 Β· 1q44
NCBI Gene: 116228Ensembl: ENSG00000203667.11HGNC: HGNC:26970UniProt: B3KM21
41PubMed Papers
21Diseases
0Drugs
15Pathogenic Variants
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
protein bindingmitochondrial respiratory chain complex IV assemblymitochondrionmitochondrial inner membranemitochondrial complex IV deficiency, nuclear type 11Isolated cytochrome C oxidase deficiencyleigh syndrome due to mitochondrial complex iv deficiencygenetic disorder
✦AI Summary

COX20 encodes an essential assembly factor for mitochondrial respiratory chain complex IV (cytochrome c oxidase) that acts as a chaperone during early stages of COX2 subunit maturation 1. The protein stabilizes newly synthesized COX2 and presents it to metallochaperones SCO1 and SCO2, facilitating incorporation of mature COX2 into the assembling complex IV holoenzyme 2. COX20 interacts directly with newly synthesized COX2, and its absence leads to accumulation of incomplete complex IV subassemblies containing COX1 but lacking COX2 2. Loss-of-function mutations in COX20 cause severe complex IV deficiency and reduce mitochondrial respiration, compromising cellular spare respiratory capacity under metabolic stress 3. Clinically, COX20 deficiency presents as an autosomal recessive mitochondrial disorder characterized by sensory neuronopathy, ataxia, hypotonia, dysarthria, and areflexia 43. The phenotypic spectrum includes early-onset developmental delay, dystonia, and visual impairment 4. COX20 is particularly important for proprioceptive sensory neurons, and its dysfunction represents a key mechanism underlying mitochondrial bioenergetic failure in peripheral sensory neuron disease 3. Multiple pathogenic variants have been identified, including missense mutations and splice site variants that eliminate full-length protein production 56.

Sources cited
1
COX20 is essential for complex IV assembly and acts as a chaperone for COX2 maturation
PMID: 23125284
2
COX20 stabilizes newly synthesized COX2 and presents it to SCO1/SCO2 metallochaperones
PMID: 24403053
3
COX20 deficiency causes complex IV deficiency and compromises mitochondrial respiration
PMID: 33751098
4
COX20 mutations cause autosomal recessive disorder with ataxia, hypotonia, and sensory neuropathy
PMID: 37095481
5
Novel splice site variants eliminate full-length COX20 protein production
PMID: 30656193
6
COX20 mutations cause sensory-dominant axonal neuropathy and static encephalopathy
PMID: 31079202
Disease Associationsβ“˜21
mitochondrial complex IV deficiency, nuclear type 11Open Targets
0.73Strong
Isolated cytochrome C oxidase deficiencyOpen Targets
0.68Moderate
leigh syndrome due to mitochondrial complex iv deficiencyOpen Targets
0.61Moderate
genetic disorderOpen Targets
0.41Moderate
mitochondrial diseaseOpen Targets
0.40Moderate
cataractOpen Targets
0.22Weak
trauma complicationOpen Targets
0.22Weak
Parkinson diseaseOpen Targets
0.22Weak
chronic intestinal pseudoobstructionOpen Targets
0.03Suggestive
glioblastoma multiformeOpen Targets
0.02Suggestive
AtaxiaOpen Targets
0.02Suggestive
synovium disorderOpen Targets
0.02Suggestive
gliomaOpen Targets
0.02Suggestive
acute lymphoblastic leukemiaOpen Targets
0.01Suggestive
Sensory neuropathyOpen Targets
0.01Suggestive
obstructive sleep apneaOpen Targets
0.01Suggestive
ulcerative colitisOpen Targets
0.01Suggestive
hyperinsulinemic hypoglycemia, familial, 4Open Targets
0.01Suggestive
heart failureOpen Targets
0.01Suggestive
ophthalmoplegiaOpen Targets
0.01Suggestive
Mitochondrial complex IV deficiency, nuclear type 11UniProt
Pathogenic Variants15
NM_198076.6(COX20):c.41A>G (p.Lys14Arg)Pathogenic
not provided|Mitochondrial complex IV deficiency, nuclear type 11|COX20-related disorder|Inborn genetic diseases|Mitochondrial disease
β˜…β˜…β˜†β˜†2026β†’ Residue 14
NM_198076.6(COX20):c.157+3G>CPathogenic
not provided|Mitochondrial complex IV deficiency, nuclear type 1|Mitochondrial complex IV deficiency, nuclear type 11|Acute myeloid leukemia|Malignant tumor of urinary bladder|Adrenocortical carcinoma, hereditary|Lung cancer|Clear cell carcinoma of kidney|Colon adenocarcinoma|Melanoma|Familial pancreatic carcinoma|Lymphoma|Uterine corpus endometrial carcinoma
β˜…β˜…β˜†β˜†2025
NM_198076.6(COX20):c.158-4_159delinsGACLikely pathogenic
Mitochondrial complex IV deficiency, nuclear type 11
β˜…β˜†β˜†β˜†2024
NM_198076.6(COX20):c.296TAT[1] (p.Leu100del)Likely pathogenic
not provided
β˜…β˜†β˜†β˜†2024β†’ Residue 100
NM_198076.6(COX20):c.53_54insAGGAT (p.Leu19fs)Likely pathogenic
Mitochondrial complex IV deficiency, nuclear type 11
β˜…β˜†β˜†β˜†2024β†’ Residue 19
NM_198076.6(COX20):c.91del (p.Arg31fs)Likely pathogenic
Mitochondrial complex IV deficiency, nuclear type 11
β˜…β˜†β˜†β˜†2024β†’ Residue 31
NM_198076.6(COX20):c.222-1G>ALikely pathogenic
Mitochondrial complex IV deficiency, nuclear type 11
β˜…β˜†β˜†β˜†2024
NM_198076.6(COX20):c.16G>T (p.Glu6Ter)Likely pathogenic
Mitochondrial complex IV deficiency, nuclear type 11
β˜…β˜†β˜†β˜†2024β†’ Residue 6
NM_198076.6(COX20):c.108T>A (p.Tyr36Ter)Likely pathogenic
Mitochondrial complex IV deficiency, nuclear type 11
β˜…β˜†β˜†β˜†2023β†’ Residue 36
NM_198076.6(COX20):c.157+1G>ALikely pathogenic
not provided
β˜…β˜†β˜†β˜†2016
NM_198076.6(COX20):c.222G>T (p.Trp74Cys)Pathogenic
Mitochondrial complex IV deficiency, nuclear type 11
β˜†β˜†β˜†β˜†2023β†’ Residue 74
NM_198076.6(COX20):c.42+1G>APathogenic
Mitochondrial complex IV deficiency, nuclear type 11
β˜†β˜†β˜†β˜†2023
NM_198076.6(COX20):c.98C>T (p.Ser33Leu)Pathogenic
Mitochondrial complex IV deficiency, nuclear type 11
β˜†β˜†β˜†β˜†2022β†’ Residue 33
NM_198076.6(COX20):c.157+7A>GPathogenic
Mitochondrial complex IV deficiency, nuclear type 11
β˜†β˜†β˜†β˜†2022
NM_198076.6(COX20):c.154A>C (p.Thr52Pro)Pathogenic
Mitochondrial complex IV deficiency, nuclear type 11
β˜†β˜†β˜†β˜†2014β†’ Residue 52
View on ClinVar β†—
Related Genes
COX17Shared pathway100%COX16Shared pathway100%COA4Shared pathway100%TMEM223Shared pathway100%PET117Shared pathway100%PET100Shared pathway100%
Tissue Expression6 tissues
Brain
100%
Ovary
30%
Liver
16%
Bone Marrow
12%
Lung
11%
Heart
11%
Gene Interaction Network
Click a node to explore
COX20COX17COX16COA4TMEM223PET117PET100
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted Β· UniProt Q5RI15
View on AlphaFold β†—
Constraintβ“˜
LOEUFβ“˜
1.93LoF Tolerant
pLIβ“˜
0.06Tolerant
Observed/Expected LoF1.55 [0.47–1.93]
RankingsWhere COX20 stands among ~20K protein-coding genes
  • #9,986of 20,598
    Most Researched41
  • #2,472of 5,498
    Most Pathogenic Variants15
  • #17,452of 17,882
    Most Constrained (LOEUF)1.93
Genes detectedCOX20
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
Human COX20 cooperates with SCO1 and SCO2 to mature COX2 and promote the assembly of cytochrome c oxidase.
PMID: 24403053
Hum Mol Genet Β· 2014
1.00
2
Clinical and genetic characteristics of children with COX20-associated mitochondrial disorder: case report and literature review.
PMID: 37095481
BMC Med Genomics Β· 2023
0.90
3
A mutation in the FAM36A gene, the human ortholog of COX20, impairs cytochrome c oxidase assembly and is associated with ataxia and muscle hypotonia.
PMID: 23125284
Hum Mol Genet Β· 2013
0.80
4
A dual role for PSIP1/LEDGF in T cell acute lymphoblastic leukemia.
PMID: 39485844
Sci Adv Β· 2024
0.70
5
Bi-allelic loss of function variants in COX20 gene cause autosomal recessive sensory neuronopathy.
PMID: 33751098
Brain Β· 2021
0.60