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GeneE
10 sources retrieved Β· Most recent: April 2026 Β· Index updated 15 days ago
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ECHDC1
ethylmalonyl-CoA decarboxylase 1
Chromosome 6 Β· 6q22.33
NCBI Gene: 55862Ensembl: ENSG00000093144.20HGNC: HGNC:21489UniProt: Q9NTX5
50PubMed Papers
20Diseases
0Drugs
3Pathogenic Variants
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
protein bindingcarboxy-lyase activityfatty acid beta-oxidationcytosolshort chain acyl-CoA dehydrogenase deficiencyAbnormality of the gastrointestinal tractpoisoninghandedness
✦AI Summary

ECHDC1 (ethylmalonyl-CoA decarboxylase 1) is a metabolite proofreading enzyme that decarboxylates ethylmalonyl-CoA, a potentially toxic metabolite, to form butyryl-CoA 1. The enzyme acts preferentially on (S)-ethylmalonyl-CoA and also exhibits lower-level methylmalonyl-CoA decarboxylase activity, but does not act on malonyl-CoA 1. ECHDC1 is particularly abundant in brown adipose tissue, liver, and kidney, and is essentially cytosolic in localization 1. Mechanistically, ECHDC1 functions to correct side activities of acetyl-CoA carboxylase and propionyl-CoA carboxylase, which produce ethylmalonyl-CoA at low rates from butyryl-CoA 1. Loss-of-function variants in ECHDC1 have been identified in humans with elevated ethylmalonic acid levels, suggesting clinical relevance in ethylmalonic aciduria 2. The gene shows disease associations across multiple contexts: it functions as a tumor suppressor in breast cancer 3, its overexpression correlates with gemcitabine resistance in bladder cancer 4, and increased expression is associated with non-alcoholic fatty liver disease through regulation of lipid metabolism 5. Additionally, ECHDC1 has been implicated in cholesterol metabolism regulation 6.

Sources cited
1
ECHDC1 decarboxylates ethylmalonyl-CoA to butyryl-CoA, acts as metabolite proofreading enzyme, tissue distribution and cellular localization
PMID: 22016388
2
Loss-of-function ECHDC1 variants identified in humans with elevated ethylmalonic acid levels
PMID: 33973257
3
ECHDC1 functions as tumor suppressor in breast cancer
PMID: 33750001
4
ECHDC1 overexpression associated with gemcitabine resistance in bladder cancer
PMID: 29391886
5
ECHDC1 increased expression associated with NAFLD and lipid metabolism regulation
PMID: 35305493
6
ECHDC1 involvement in cholesterol metabolism regulation
PMID: 38417553
Disease Associationsβ“˜20
short chain acyl-CoA dehydrogenase deficiencyOpen Targets
0.36Weak
Abnormality of the gastrointestinal tractOpen Targets
0.34Weak
poisoningOpen Targets
0.28Weak
handednessOpen Targets
0.28Weak
familial hypercholesterolemiaOpen Targets
0.07Suggestive
hypertriglyceridemia 2Open Targets
0.07Suggestive
hyperlipidemia due to hepatic triglyceride lipase deficiencyOpen Targets
0.06Suggestive
Hyperlipoproteinemia type 1Open Targets
0.06Suggestive
homozygous familial hypercholesterolemiaOpen Targets
0.06Suggestive
thyroid hormone metabolism, abnormal, 2Open Targets
0.06Suggestive
Combined hyperlipidemiaOpen Targets
0.06Suggestive
sitosterolemia 2Open Targets
0.05Suggestive
hypoalphalipoproteinemia, primary, 1Open Targets
0.05Suggestive
fish eye diseaseOpen Targets
0.05Suggestive
Fish-eye diseaseOpen Targets
0.05Suggestive
hypertensionOpen Targets
0.05Suggestive
breast cancerOpen Targets
0.05Suggestive
familial apolipoprotein C-II deficiencyOpen Targets
0.05Suggestive
coronary artery diseaseOpen Targets
0.05Suggestive
hypercholesterolemia, autosomal dominant, 3Open Targets
0.04Suggestive
Pathogenic Variants3
NM_001002030.2(ECHDC1):c.498-40AG[2]Likely pathogenic
Deficiency of butyryl-CoA dehydrogenase
β˜…β˜†β˜†β˜†2019
NM_001002030.2(ECHDC1):c.389T>C (p.Met130Thr)Likely pathogenic
Deficiency of butyryl-CoA dehydrogenase
β˜…β˜†β˜†β˜†2019β†’ Residue 130
NM_001002030.2(ECHDC1):c.221-4_222delinsTALikely pathogenic
Deficiency of butyryl-CoA dehydrogenase
β˜…β˜†β˜†β˜†2019
View on ClinVar β†—
Related Genes
ECI1Shared pathway100%ECH1Shared pathway100%ECI2Shared pathway100%ECHDC2Shared pathway100%HADHProtein interaction98%HIBCHProtein interaction96%
Tissue Expression6 tissues
Heart
100%
Liver
100%
Brain
91%
Lung
88%
Ovary
44%
Bone Marrow
32%
Gene Interaction Network
Click a node to explore
ECHDC1ECI1ECH1ECI2ECHDC2HADHHIBCH
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted Β· UniProt Q9NTX5
View on AlphaFold β†—
Constraintβ“˜
LOEUFβ“˜
1.45LoF Tolerant
pLIβ“˜
0.00Tolerant
Observed/Expected LoF1.07 [0.79–1.45]
RankingsWhere ECHDC1 stands among ~20K protein-coding genes
  • #8,800of 20,598
    Most Researched50
  • #4,058of 5,498
    Most Pathogenic Variants3
  • #14,870of 17,882
    Most Constrained (LOEUF)1.45
Genes detectedECHDC1
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
The RNF146 and ECHDC1 genes as candidates for inherited breast and ovarian cancer in Jewish Ashkenazi women.
PMID: 19517271
Fam Cancer Β· 2009
1.00
2
Multi-modal meta-analysis of cancer cell line omics profiles identifies ECHDC1 as a novel breast tumor suppressor.
PMID: 33750001
Mol Syst Biol Β· 2021
0.90
3
Variants in the ethylmalonyl-CoA decarboxylase (ECHDC1) gene: a novel player in ethylmalonic aciduria?
PMID: 33973257
J Inherit Metab Dis Β· 2021
0.80
4
Transcriptomic analysis reveals a novel regulatory factor of ECHDC1 involved in lipid metabolism of non-alcoholic fatty liver disease.
PMID: 35305493
Biochem Biophys Res Commun Β· 2022
0.70
5
Silencing of
PMID: 29391886
Oncol Lett Β· 2018
0.60