NM_000182.5(HADHA):c.1528G>C (p.Glu510Gln)Pathogenic
Mitochondrial trifunctional protein deficiency|LCHAD deficiency with maternal acute fatty liver of pregnancy|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|not provided|Inborn genetic diseases|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency;Mitochondrial trifunctional protein deficiency|HADHA-related disorder|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency;Mitochondrial trifunctional protein deficiency 1|Metabolic disease
β
β
ββ2026β Residue 510
NM_000182.5(HADHA):c.919-2A>GPathogenic
Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|not provided|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency;Mitochondrial trifunctional protein deficiency|Mitochondrial trifunctional protein deficiency 1;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2026
NM_000182.5(HADHA):c.1678C>T (p.Arg560Ter)Pathogenic
Mitochondrial trifunctional protein deficiency|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency 1|Mitochondrial trifunctional protein deficiency 1;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|not provided
β
β
ββ2026β Residue 560
NM_000182.5(HADHA):c.1793_1794del (p.His598fs)Pathogenic
Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency;Mitochondrial trifunctional protein deficiency|Mitochondrial trifunctional protein deficiency|not provided|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency;Mitochondrial trifunctional protein deficiency 1|Mitochondrial trifunctional protein deficiency 1
β
β
ββ2025β Residue 598
NM_000182.5(HADHA):c.180+3A>GPathogenic
not provided|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency 1|Mitochondrial trifunctional protein deficiency 1;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2025
NM_000182.5(HADHA):c.2026C>T (p.Arg676Cys)Pathogenic
Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency 1
β
β
ββ2025β Residue 676
NM_000182.5(HADHA):c.1086-3_1092delPathogenic
Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2025
NM_000182.5(HADHA):c.314+1G>CLikely pathogenic
Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2025
NM_000182.5(HADHA):c.1195C>T (p.Arg399Ter)Pathogenic
not provided|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2025β Residue 399
NM_000182.5(HADHA):c.2027G>A (p.Arg676His)Pathogenic
Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency;Mitochondrial trifunctional protein deficiency|not provided|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency;Mitochondrial trifunctional protein deficiency 1
β
β
ββ2025β Residue 676
NM_000182.5(HADHA):c.1690-2A>GPathogenic
Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|not provided|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency;Mitochondrial trifunctional protein deficiency
β
β
ββ2025
NM_000182.5(HADHA):c.1811del (p.Gly604fs)Pathogenic
Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|not provided|Mitochondrial trifunctional protein deficiency|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2025β Residue 604
NM_000182.5(HADHA):c.1432del (p.Ala478fs)Pathogenic
Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2025β Residue 478
NM_000182.5(HADHA):c.914T>A (p.Ile305Asn)Pathogenic
not provided|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency 1|Mitochondrial trifunctional protein deficiency 1;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2025β Residue 305
NM_000182.5(HADHA):c.314+2T>GLikely pathogenic
Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency;Mitochondrial trifunctional protein deficiency|not provided|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2025
NM_000182.5(HADHA):c.180+1G>APathogenic
Mitochondrial trifunctional protein deficiency|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency 1
β
β
ββ2025
NM_000182.5(HADHA):c.2225_2228dup (p.Phe744fs)Pathogenic
Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency
β
β
ββ2025β Residue 744
NM_000182.5(HADHA):c.1814_1815del (p.Lys605fs)Pathogenic
not provided|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2025β Residue 605
NM_000182.5(HADHA):c.1916_1919dup (p.Glu641fs)Pathogenic
not provided|See cases|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency 1;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2025β Residue 641
NM_000182.5(HADHA):c.676+2T>CPathogenic
Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency|Mitochondrial trifunctional protein deficiency;Long chain 3-hydroxyacyl-CoA dehydrogenase deficiency
β
β
ββ2025