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10 sources retrieved · Most recent: April 2026 · Index updated 14 days ago
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IL1RAP
interleukin 1 receptor accessory protein
Chromosome 3 · 3q28
NCBI Gene: 3556Ensembl: ENSG00000196083.12HGNC: HGNC:5995UniProt: A8K6K4
127PubMed Papers
20Diseases
3Drugs
0Pathogenic Variants
FUNCTIONAL ROLE
Receptor
CLINICAL
FDA Approved Target
DATA QUALITY
✓ Experimental GO Evidence✓ Swiss-Prot Reviewed
interleukin-1-mediated signaling pathwayprotein bindinginterleukin-33-mediated signaling pathwaypositive regulation of canonical NF-kappaB signal transductionpsoriasispsoriasis vulgarisgeneralized pustular psoriasisimmune system disease
✦AI Summary

IL1RAP (interleukin-1 receptor accessory protein) functions as an essential coreceptor for IL-1, IL-33, and IL-36 signaling pathways 1. Unlike canonical IL-1 signaling, IL1RAP is required for Src phosphorylation by IL1B [UniProt reference]. The protein mediates inflammatory responses through positive regulation of MAPK cascades and NF-κB signal transduction [GO annotations]. Mechanistically, IL1RAP regulates multiple pathways: in Ewing sarcoma, it maintains redox homeostasis by enhancing cystine uptake and activating transsulfuration pathways for cysteine synthesis 2. In cardiovascular and fibrotic diseases, IL1RAP blockade reduces inflammatory cytokine production (IL-6, IL-8, MCP-1) and adhesion molecule expression in endothelial cells 3, while limiting leucocyte recruitment and plaque inflammation in atherosclerosis 4. Clinically, IL1RAP represents a promising therapeutic target across multiple malignancies and inflammatory diseases. IL1RAP is highly expressed on acute myeloid leukemia stem cells but not normal hematopoietic stem cells, enabling selective targeting via T cell engagers 5. Anti-IL1RAP antibodies show efficacy in systemic sclerosis-associated fibrosis 1, pancreatic cancer (median OS 13.2 months combined with chemotherapy) 6, and myocarditis by reducing cardiac inflammation and preserving function 7. These findings establish IL1RAP as a clinically actionable immunotherapeutic target.

Sources cited
1
IL1RAP is an essential coreceptor for IL-1, IL-33, and IL-36 receptor signaling
PMID: 38594058
2
IL1RAP maintains redox homeostasis via cystine uptake enhancement and transsulfuration pathway activation in Ewing sarcoma
PMID: 34021002
3
IL1RAP blockade reduces inflammatory cytokine production and adhesion molecule expression in endothelial cells
PMID: 40371594
4
IL1RAP blockade reduces plaque burden and limits leucocyte recruitment in atherosclerosis
PMID: 38563353
5
IL1RAP is highly expressed on AML stem cells but not normal HSCs, enabling selective targeting via T cell engagers
PMID: 39143574
6
Anti-IL1RAP antibody nadunolimab combined with gemcitabine/nab-paclitaxel achieves median OS of 13.2 months in advanced pancreatic cancer
PMID: 39385434
7
IL1RAP blockade reduces cardiac inflammation and preserves heart function in viral and autoimmune myocarditis
PMID: 39513273
Disease Associationsⓘ20
psoriasisOpen Targets
0.48Moderate
psoriasis vulgarisOpen Targets
0.39Weak
generalized pustular psoriasisOpen Targets
0.38Weak
immune system diseaseOpen Targets
0.37Weak
pustular psoriasisOpen Targets
0.37Weak
chronic obstructive pulmonary diseaseOpen Targets
0.36Weak
diabetes mellitusOpen Targets
0.26Weak
hidradenitis suppurativaOpen Targets
0.25Weak
response to antihypertensive drugOpen Targets
0.24Weak
ulcerative colitisOpen Targets
0.22Weak
Netherton syndromeOpen Targets
0.18Weak
myopiaOpen Targets
0.11Weak
pathological myopiaOpen Targets
0.11Weak
acute myeloid leukemiaOpen Targets
0.11Weak
asthmaOpen Targets
0.11Weak
Crohn's diseaseOpen Targets
0.10Weak
atopic eczemaOpen Targets
0.10Weak
palmoplantar pustulosisOpen Targets
0.10Weak
neoplasmOpen Targets
0.10Suggestive
Ewing sarcomaOpen Targets
0.08Suggestive
Pathogenic Variants
No pathogenic variants reported on ClinVar for this gene.
View on ClinVar ↗
Drug Targets3
ASTEGOLIMABPhase III
IL-33 receptor (ST2) inhibitor
chronic obstructive pulmonary disease
IMSIDOLIMABPhase III
IL36 receptor antagonist
generalized pustular psoriasis
SPESOLIMABApproved
IL36 receptor antagonist
pustular psoriasis
Related Genes
IL1BProtein interaction100%PTPRDProtein interaction99%MYD88Protein interaction97%PTPRSProtein interaction95%IRAK1Protein interaction93%IL36AProtein interaction91%
Tissue Expression6 tissues
Liver
100%
Bone Marrow
27%
Lung
21%
Brain
12%
Heart
9%
Ovary
5%
Gene Interaction Network
Click a node to explore
IL1RAPIL1BPTPRDMYD88PTPRSIRAK1IL36A
PROTEIN STRUCTURE
Preparing viewer…
PDB7FCC · 2.14 Å · X-ray
View on RCSB ↗
Constraintⓘ
LOEUFⓘ
0.76LoF Tolerant
pLIⓘ
0.00Tolerant
Observed/Expected LoF0.54 [0.39–0.76]
RankingsWhere IL1RAP stands among ~20K protein-coding genes
  • #3,691of 20,598
    Most Researched127 · top quartile
  • #923of 1,025
    FDA-Approved Drug Targets1
  • #6,097of 17,882
    Most Constrained (LOEUF)0.76
Genes detectedIL1RAP
Sources retrieved10 papers
Response time—
📄 Sources
10▼
1
IL1RAP-specific T cell engager depletes acute myeloid leukemia stem cells.
PMID: 39143574
J Hematol Oncol · 2024
1.00
2
Combined inhibition of IL-1, IL-33 and IL-36 signalling by targeting IL1RAP ameliorates skin and lung fibrosis in preclinical models of systemic sclerosis.
PMID: 38594058
Ann Rheum Dis · 2024
0.90
3
Proteomic Screens for Suppressors of Anoikis Identify IL1RAP as a Promising Surface Target in Ewing Sarcoma.
PMID: 34021002
Cancer Discov · 2021
0.80
4
IL1RAP Expression in Human Atherosclerosis: A Target of Novel Antibodies to Reduce Vascular Inflammation and Adhesion.
PMID: 40371594
J Am Heart Assoc · 2025
0.70
5
Interleukin-1 receptor accessory protein blockade limits the development of atherosclerosis and reduces plaque inflammation.
PMID: 38563353
Cardiovasc Res · 2024
0.60