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GeneE
10 sources retrieved Β· Most recent: April 2026 Β· Index updated 15 days ago
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KIAA0753
KIAA0753
Chromosome 17 Β· 17p13.1
NCBI Gene: 9851Ensembl: ENSG00000198920.11HGNC: HGNC:29110UniProt: Q2KHM9
42PubMed Papers
23Diseases
0Drugs
46Pathogenic Variants
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
centriolar satellitecentrosomecilium assemblycytosolic ciliogenesisJoubert syndromeshort-rib thoracic dysplasia 21 without polydactylyJoubert syndrome with orofaciodigital defectJeune syndrome
✦AI Summary

KIAA0753 is a centrosomal protein essential for primary ciliogenesis and centriole biogenesis 1. It functions as a centriolar satellite protein that positively regulates CEP63 centrosomal localization and promotes CDK2 centrosomal recruitment 2. KIAA0753 is recruited to centrioles by CEP120 and forms a complex with OFD1 and FOR20 at pericentriolar satellites, possessing microtubule-stabilizing activity 34. Loss of KIAA0753 blocks primary ciliogenesis and impairs sonic hedgehog (SHH) pathway signaling, which is critical for neural and skeletal development 1. KIAA0753 enhances osteoblast differentiation through direct interaction with SHH, activating Hedgehog signaling and protecting Gli2 from ubiquitination 5. Pathogenic KIAA0753 variants cause multiple ciliopathies with overlapping phenotypes, including Joubert syndrome (cerebellar vermis hypoplasia, developmental delay) 14, orofaciodigital syndrome (facial and digital abnormalities) 36, and short-rib thoracic dysplasia with skeletal dysplasia 7. Patient fibroblasts demonstrate deficient primary ciliation and blunted SHH pathway responses 1. KIAA0753 variants also associate with ciliary dyskinesia and neuro-degenerative complications 8. The phenotypic heterogeneity reflects variable functional competence of mutant proteins in promoting ciliogenesis and centrosomal localization.

Sources cited
1
KIAA0753 is required for primary ciliogenesis; ablation blocks ciliogenesis and SHH pathway activity; patient variants impair ciliogenic function
PMID: 34523780
2
KIAA0753 positively regulates centriole duplication and CEP63 centrosomal localization; identified as centriolar satellite protein regulator
PMID: 24613305
3
KIAA0753 associates with centrosomes and pericentriolar satellites; forms complex with FOR20 and OFD1; has microtubule-stabilizing activity
PMID: 26643951
4
CEP120 recruits KIAA0753 to centrioles; CEP120-KIAA0753 interaction required for neuronal differentiation and germinal zone exit in developing cerebellum
PMID: 34711653
5
KIAA0753 promotes osteoblast differentiation by interacting with SHH and Gli2, activating Hedgehog pathway and protecting Gli2 from ubiquitination in diabetes
PMID: 39245790
6
KIAA0753 mutations cause short-rib skeletal dysplasia; expressed in fetal growth plate; zebrafish with kiaa0753 mutation show altered cartilage patterning
PMID: 29138412
7
KIAA0753 mutations identified in orofaciodigital syndrome; KIAA0753-FOPNL-OFD1 complex regulates centriole elongation
PMID: 28289185
8
KIAA0753-related skeletal ciliopathy phenotype includes short stature, developmental delay, CNS anomalies, cone-rod dystrophy, and ciliary dyskinesia
PMID: 34016807
Disease Associationsβ“˜23
Joubert syndromeOpen Targets
0.69Moderate
short-rib thoracic dysplasia 21 without polydactylyOpen Targets
0.67Moderate
Joubert syndrome with orofaciodigital defectOpen Targets
0.67Moderate
Jeune syndromeOpen Targets
0.59Moderate
Joubert syndrome 38Open Targets
0.58Moderate
genetic disorderOpen Targets
0.47Moderate
hypothyroidismOpen Targets
0.37Weak
orofaciodigital syndrome type 6Open Targets
0.37Weak
neurodegenerative diseaseOpen Targets
0.34Weak
coronary artery diseaseOpen Targets
0.25Weak
hypertensionOpen Targets
0.22Weak
alopecia areataOpen Targets
0.20Weak
response to xenobiotic stimulusOpen Targets
0.15Weak
endocrine system diseaseOpen Targets
0.11Weak
diabetes mellitusOpen Targets
0.09Suggestive
amblyopiaOpen Targets
0.09Suggestive
eye diseaseOpen Targets
0.09Suggestive
type 2 diabetes mellitusOpen Targets
0.07Suggestive
attention deficit hyperactivity disorderOpen Targets
0.07Suggestive
hereditary attention deficit-hyperactivity disorderOpen Targets
0.06Suggestive
Joubert syndrome 38UniProt
Orofaciodigital syndrome 15UniProt
Short-rib thoracic dysplasia 21 without polydactylyUniProt
Pathogenic Variants46
NM_014804.3(KIAA0753):c.757C>T (p.Arg253Ter)Pathogenic
not provided|Inborn genetic diseases|Orofaciodigital syndrome XV;Short-rib thoracic dysplasia 21 without polydactyly
β˜…β˜…β˜†β˜†2025β†’ Residue 253
NM_014804.3(KIAA0753):c.1891A>T (p.Lys631Ter)Pathogenic
Orofaciodigital syndrome XV|not specified|not provided|Joubert syndrome 38
β˜…β˜…β˜†β˜†2025β†’ Residue 631
NM_014804.3(KIAA0753):c.2656C>T (p.Arg886Ter)Pathogenic
not provided|Orofaciodigital syndrome XV|KIAA0753-related disorder|Short-rib thoracic dysplasia 21 without polydactyly;Orofaciodigital syndrome XV
β˜…β˜…β˜†β˜†2025β†’ Residue 886
NM_014804.3(KIAA0753):c.661C>T (p.Arg221Ter)Pathogenic
not provided|Orofaciodigital syndrome XV;Short-rib thoracic dysplasia 21 without polydactyly
β˜…β˜…β˜†β˜†2025β†’ Residue 221
NM_014804.3(KIAA0753):c.970C>T (p.Arg324Ter)Pathogenic
Jeune thoracic dystrophy;Joubert syndrome|Jeune thoracic dystrophy|not provided|Short-rib thoracic dysplasia 21 without polydactyly|Orofaciodigital syndrome XV|Orofaciodigital syndrome XV;Short-rib thoracic dysplasia 21 without polydactyly
β˜…β˜…β˜†β˜†2024β†’ Residue 324
NM_014804.3(KIAA0753):c.799C>T (p.Arg267Ter)Pathogenic
Inborn genetic diseases|not provided
β˜…β˜…β˜†β˜†2024β†’ Residue 267
NM_014804.3(KIAA0753):c.1323T>A (p.Tyr441Ter)Pathogenic
not provided
β˜…β˜…β˜†β˜†2023β†’ Residue 441
NM_014804.3(KIAA0753):c.1481del (p.Lys494fs)Pathogenic
Joubert syndrome 38|not provided
β˜…β˜…β˜†β˜†2023β†’ Residue 494
NM_014804.3(KIAA0753):c.1571_1572del (p.Arg524fs)Pathogenic
not specified|Short-rib thoracic dysplasia 21 without polydactyly|not provided
β˜…β˜…β˜†β˜†2022β†’ Residue 524
NM_014804.3(KIAA0753):c.320_321del (p.Asp107fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2026β†’ Residue 107
NM_014804.3(KIAA0753):c.2483dup (p.His828fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 828
NM_014804.3(KIAA0753):c.93+1G>ALikely pathogenic
not provided
β˜…β˜†β˜†β˜†2025
NM_014804.3(KIAA0753):c.832G>T (p.Glu278Ter)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 278
NM_014804.3(KIAA0753):c.1104+1G>ALikely pathogenic
not provided
β˜…β˜†β˜†β˜†2025
NM_014804.3(KIAA0753):c.148C>T (p.Arg50Ter)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 50
NM_014804.3(KIAA0753):c.93+2T>ALikely pathogenic
not provided
β˜…β˜†β˜†β˜†2025
NM_014804.3(KIAA0753):c.1315+1G>TLikely pathogenic
not provided
β˜…β˜†β˜†β˜†2025
NM_014804.3(KIAA0753):c.205_206dup (p.Tyr70fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 70
NM_014804.3(KIAA0753):c.1722del (p.Trp574fs)Likely pathogenic
Short-rib thoracic dysplasia 21 without polydactyly;Orofaciodigital syndrome XV;Joubert syndrome 38
β˜…β˜†β˜†β˜†2025β†’ Residue 574
NM_014804.3(KIAA0753):c.1324C>T (p.Gln442Ter)Likely pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 442
View on ClinVar β†—
Related Genes
CEP63Protein interaction82%PCM1Protein interaction77%CCDC14Protein interaction75%CEP135Protein interaction71%OFD1Protein interaction54%C2CD3Shared pathway40%
Tissue Expression6 tissues
Ovary
100%
Bone Marrow
59%
Lung
49%
Heart
40%
Liver
38%
Brain
35%
Gene Interaction Network
Click a node to explore
KIAA0753CEP63PCM1CCDC14CEP135OFD1C2CD3
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted Β· UniProt Q2KHM9
View on AlphaFold β†—
Constraintβ“˜
LOEUFβ“˜
1.07LoF Tolerant
pLIβ“˜
0.00Tolerant
Observed/Expected LoF0.89 [0.73–1.07]
RankingsWhere KIAA0753 stands among ~20K protein-coding genes
  • #9,892of 20,598
    Most Researched42
  • #1,413of 5,498
    Most Pathogenic Variants46
  • #10,822of 17,882
    Most Constrained (LOEUF)1.07
Genes detectedKIAA0753
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
Genetic and phenotypic heterogeneity in KIAA0753-related ciliopathies.
PMID: 34523780
Am J Med Genet A Β· 2022
1.00
2
Proximity interactions among centrosome components identify regulators of centriole duplication.
PMID: 24613305
Curr Biol Β· 2014
0.90
3
Novel KIAA0753 mutations extend the phenotype of skeletal ciliopathies.
PMID: 29138412
Sci Rep Β· 2017
0.80
4
CEP120-mediated KIAA0753 recruitment onto centrioles is required for timely neuronal differentiation and germinal zone exit in the developing cerebellum.
PMID: 34711653
Genes Dev Β· 2021
0.70
5
OFIP/KIAA0753 forms a complex with OFD1 and FOR20 at pericentriolar satellites and centrosomes and is mutated in one individual with oral-facial-digital syndrome.
PMID: 26643951
Hum Mol Genet Β· 2016
0.60