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10 sources retrieved Β· Most recent: April 2026 Β· Index updated 15 days ago
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NDUFA1
NADH:ubiquinone oxidoreductase subunit A1
Chromosome X Β· Xq24
NCBI Gene: 4694Ensembl: ENSG00000125356.8HGNC: HGNC:7683UniProt: O15239
36PubMed Papers
21Diseases
3Drugs
3Pathogenic Variants
FUNCTIONAL ROLE
Hub GeneTransporter
CLINICAL
FDA Approved TargetOMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
respiratory chain complex Imitochondrial inner membranemitochondrionmitochondrial membranemitochondrial complex I deficiencymitochondrial complex I deficiency, nuclear type 12type 2 diabetes mellitusdiabetes mellitus
✦AI Summary

NDUFA1 is an X-linked accessory subunit of mitochondrial Complex I (NADH:ubiquinone oxidoreductase) that functions in the transfer of electrons from NADH to ubiquinone within the respiratory chain 1. Although not directly involved in catalysis, NDUFA1 is essential for Complex I assembly, stability, and activity 2. The protein localizes to the mitochondrial inner membrane and contains lipid-exposed surfaces critical for stabilizing Complex I structure through interactions with cardiolipin 3. Pathogenic variants in NDUFA1 cause mitochondrial Complex I deficiency, presenting clinically as mitochondrial encephalomyopathy, Leigh syndrome, myoclonic epilepsy, and developmental delay 2. Recent studies identified NDUFA1 as a biomarker for Alzheimer's disease, with reduced protein levels associated with impaired mitochondrial function in the AD hippocampus 4. The p.Gly32Arg variant has been linked to early-onset dementia in multiple families 5. Additionally, NDUFA1 appears in optic atrophy presentations through recessive variants affecting accessory Complex I subunits 6. Beyond inherited mitochondrial disease, elevated NDUFA1 expression associates with poor prognosis in esophageal cancer through PI3K/Akt pathway activation 7. NDUFA1 also mediates ferroptosis resistance through FSP1 interaction; its suppression by IDH1-R132H mutation aggravates cisplatin-induced acute kidney injury 8.

Sources cited
1
NDUFA1 gene isolation, mapping to Xq24, genomic structure, and homology to bovine Complex I subunit
PMID: 8938439
2
X-linked NDUFA1 mutations (p.Gly8Arg, p.Arg37Ser) cause Complex I deficiency and mitochondrial encephalomyopathy; mutations impair Complex I assembly and stability
PMID: 17262856
3
NDUFA1 lipid-exposed surfaces interact with cardiolipin to stabilize Complex I; kingdom-specific lipid unsaturation affects NDUFA1 sequence evolution and Complex I stability
PMID: 40016208
4
NDUFA1 identified as biomarker for Alzheimer's disease with reduced protein levels and diagnostic potential through mitochondrial dysfunction analysis
PMID: 40329774
5
NDUFA1 p.Gly32Arg variant associated with early-onset dementia in multiple families
PMID: 35131137
6
Recessive NDUFA1 variants cause optic atrophy and inherited optic neuropathies as accessory Complex I subunit defects
PMID: 41234160
7
Elevated NDUFA1 expression in esophageal cancer associated with poor prognosis; NDUFA1 knockdown inhibits tumor growth via PI3K/Akt pathway
PMID: 39937347
8
NDUFA1 suppression by IDH1-R132H mutation disrupts NDUFA1-FSP1 interaction, promoting ferroptosis and cisplatin-induced acute kidney injury
PMID: 39306640
Disease Associationsβ“˜21
mitochondrial complex I deficiencyOpen Targets
0.75Strong
mitochondrial complex I deficiency, nuclear type 12Open Targets
0.66Moderate
type 2 diabetes mellitusOpen Targets
0.61Moderate
diabetes mellitusOpen Targets
0.60Moderate
mitochondrial complex I deficiency, nuclear type 1Open Targets
0.56Moderate
mitochondrial diseaseOpen Targets
0.55Moderate
neurodegenerative diseaseOpen Targets
0.53Moderate
polycystic ovary syndromeOpen Targets
0.41Moderate
gestational diabetesOpen Targets
0.41Moderate
Insulin resistanceOpen Targets
0.40Moderate
obesityOpen Targets
0.40Weak
prediabetes syndromeOpen Targets
0.40Weak
metabolic syndromeOpen Targets
0.39Weak
type 1 diabetes mellitusOpen Targets
0.39Weak
Disorder of lipid metabolismOpen Targets
0.38Weak
agingOpen Targets
0.37Weak
prostate cancerOpen Targets
0.36Weak
COVID-19Open Targets
0.36Weak
abnormal glucose toleranceOpen Targets
0.36Weak
metabolic diseaseOpen Targets
0.35Weak
Mitochondrial complex I deficiency, nuclear type 12UniProt
Pathogenic Variants3
NM_004541.4(NDUFA1):c.127T>C (p.Tyr43His)Likely pathogenic
Inborn genetic diseases
β˜…β˜†β˜†β˜†2013β†’ Residue 43
NM_004541.4(NDUFA1):c.22G>C (p.Gly8Arg)Pathogenic
Mitochondrial complex I deficiency, nuclear type 12
β˜†β˜†β˜†β˜†2007β†’ Residue 8
NM_004541.4(NDUFA1):c.111G>C (p.Arg37Ser)Pathogenic
Mitochondrial complex I deficiency, nuclear type 12
β˜†β˜†β˜†β˜†2007β†’ Residue 37
View on ClinVar β†—
Drug Targets3
ME-344Phase I/II
Mitochondrial complex I (NADH dehydrogenase) inhibitor
breast cancer
METFORMINApproved
Mitochondrial complex I (NADH dehydrogenase) inhibitor
diabetes mellitus
METFORMIN HYDROCHLORIDEApproved
Mitochondrial complex I (NADH dehydrogenase) inhibitor
type 2 diabetes mellitus
Related Genes
NDUFB5Protein interaction100%NDUFC1Protein interaction100%NDUFB8Protein interaction100%NDUFS6Protein interaction100%NDUFB2Protein interaction100%NDUFB7Protein interaction100%
Tissue Expression6 tissues
Heart
100%
Liver
39%
Brain
35%
Bone Marrow
25%
Lung
22%
Ovary
18%
Gene Interaction Network
Click a node to explore
NDUFA1NDUFB5NDUFC1NDUFB8NDUFS6NDUFB2NDUFB7
PROTEIN STRUCTURE
Preparing viewer…
PDB9CWT Β· 3.44 Γ… Β· EM
View on RCSB β†—
RankingsWhere NDUFA1 stands among ~20K protein-coding genes
  • #10,824of 20,598
    Most Researched36
  • #680of 1,025
    FDA-Approved Drug Targets2
  • #4,096of 5,498
    Most Pathogenic Variants3
Genes detectedNDUFA1
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
The IDH1-R132H mutation aggravates cisplatin-induced acute kidney injury by promoting ferroptosis through disrupting NDUFA1 and FSP1 interaction.
PMID: 39306640
Cell Death Differ Β· 2025
1.00
2
Pan-cancer and multi-omics analysis: NDUFA1 is a potential therapeutic target and prognostic marker for esophageal cancer.
PMID: 39937347
Cell Biol Toxicol Β· 2025
0.90
3
Identification of NDUFV2, NDUFS7, OPA1, and NDUFA1 as biomarkers for Alzheimer's disease: Insights from oxidative stress and mitochondrial dysfunction in the hippocampus.
PMID: 40329774
J Alzheimers Dis Β· 2025
0.80
4
NDUFA1 p.Gly32Arg variant in early-onset dementia.
PMID: 35131137
Neurobiol Aging Β· 2022
0.70
5
Isolation, mapping, and genomic structure of an X-linked gene for a subunit of human mitochondrial complex I.
PMID: 8938439
Genomics Β· 1996
0.60