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GeneE
4 sources retrieved Β· Most recent: April 2026 Β· Index updated 14 days ago
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NDUFAF8
NADH:ubiquinone oxidoreductase complex assembly factor 8
Chromosome 17 Β· 17q25.3
NCBI Gene: 284184Ensembl: ENSG00000224877.4HGNC: HGNC:33551UniProt: A1L188
10PubMed Papers
21Diseases
0Drugs
5Pathogenic Variants
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
protein bindingmitochondrial respiratory chain complex I assemblymitochondrionmitochondrial matrixmitochondrial complex I deficiency, nuclear type 34mitochondrial diseaseLeigh syndromemitochondrial complex I deficiency
✦AI Summary

NDUFAF8 is a mitochondrial assembly factor essential for proper biogenesis of respiratory complex I. It functions as a stabilizer of NDUFAF5 during the early stages of complex I assembly in the mitochondrial matrix 1. Mechanistically, NDUFAF8 acts as a scaffolding protein that facilitates the incorporation of core and accessory subunits into the nascent complex I structure, as evidenced by complexome profiling studies showing stalled assembly intermediates in patient fibroblasts 2. Pathogenic variants in NDUFAF8 cause mitochondrial complex I deficiency with diverse clinical manifestations. Biallelic mutations have been associated with Leigh syndrome, characterized by symmetrical neuroimaging lesions in basal ganglia, thalamus, and brainstem, alongside developmental regression and premature death 23. More recently, NDUFAF8 deficiency has been recognized as a novel genetic cause of autosomal recessive Leber Hereditary Optic Neuropathy (arLHON) with subacute vision loss, broadening the phenotypic spectrum beyond classical Leigh presentation 4. Rare variants have also been tentatively associated with craniofacial anomalies and cardiac defects in complex genetic backgrounds 5. Clinically, NDUFAF8 genetic testing should be considered in patients with unexplained complex I deficiency, particularly those presenting with optic neuropathy or early-onset neurodegeneration, warranting comprehensive genomic screening including intronic sequences for diagnostic completeness 24.

Sources cited
1
NDUFAF8 is involved in mitochondrial complex I assembly and stabilizes NDUFAF5
PMID: 27499296
2
Biallelic NDUFAF8 mutations cause Leigh syndrome with isolated complex I deficiency and assembly defect; lentiviral correction ameliorates biochemical deficiency
PMID: 31866046
3
NDUFAF8 deficiency is a rare cause of mitochondrial complex I deficiency and Leigh syndrome with premature death; only three cases described before this report
PMID: 39921456
4
NDUFAF8 variants associated with autosomal recessive Leber Hereditary Optic Neuropathy phenotype with subacute vision loss; identified in 31 patients across 11 different complex I-related genes
PMID: 41234160
5
Rare frameshift mutation in NDUFAF8 identified in Goldenhar syndrome family with limited segregation, possibly implicating the gene in craniofacial anomalies
PMID: 41898833
Disease Associationsβ“˜21
mitochondrial complex I deficiency, nuclear type 34Open Targets
0.75Strong
mitochondrial diseaseOpen Targets
0.48Moderate
Leigh syndromeOpen Targets
0.42Moderate
mitochondrial complex I deficiencyOpen Targets
0.37Weak
obesityOpen Targets
0.26Weak
genetic disorderOpen Targets
0.16Weak
hypertensionOpen Targets
0.14Weak
response to xenobiotic stimulusOpen Targets
0.14Weak
hyperinsulinemic hypoglycemia, familial, 4Open Targets
0.01Suggestive
cancerOpen Targets
0.01Suggestive
asthmaOpen Targets
0.00Suggestive
breast cancerOpen Targets
0.00Suggestive
neoplasmOpen Targets
0.00Suggestive
Leber hereditary optic neuropathy, autosomal recessiveOpen Targets
0.00Suggestive
invasive breast ductal carcinomaOpen Targets
0.00Suggestive
Parkinson diseaseOpen Targets
0.00Suggestive
Salmonella InfectionsOpen Targets
0.00Suggestive
Wilson diseaseOpen Targets
0.00Suggestive
gastric cancerOpen Targets
0.00Suggestive
lung cancerOpen Targets
0.00Suggestive
Mitochondrial complex I deficiency, nuclear type 34UniProt
Pathogenic Variants5
NM_001086521.2(NDUFAF8):c.195+271C>TPathogenic
Mitochondrial complex I deficiency, nuclear type 34|Mitochondrial disease|not provided|NDUFAF8-related disorder
β˜…β˜…β˜†β˜†2025
NM_001086521.2(NDUFAF8):c.1A>C (p.Met1Leu)Pathogenic
Mitochondrial complex I deficiency, nuclear type 34
β˜…β˜…β˜†β˜†2022β†’ Residue 1
NM_001086521.2(NDUFAF8):c.165C>G (p.Phe55Leu)Likely pathogenic
Mitochondrial disease|Mitochondrial complex I deficiency, nuclear type 34
β˜…β˜†β˜†β˜†2019β†’ Residue 55
NM_001086521.2(NDUFAF8):c.1A>G (p.Met1Val)Pathogenic
Mitochondrial disease|Mitochondrial complex I deficiency, nuclear type 34
β˜…β˜†β˜†β˜†2019β†’ Residue 1
NM_001086521.2(NDUFAF8):c.45_52dup (p.Phe18fs)Pathogenic
Mitochondrial disease|Mitochondrial complex I deficiency, nuclear type 34
β˜…β˜†β˜†β˜†2019β†’ Residue 18
View on ClinVar β†—
Related Genes
TMEM186Shared pathway100%NDUFAF3Shared pathway100%TIMMDC1Shared pathway100%NDUFAF7Shared pathway100%FOXRED1Shared pathway100%TMEM126BShared pathway100%
Tissue Expression6 tissues
Liver
100%
Heart
65%
Ovary
51%
Bone Marrow
49%
Lung
44%
Brain
41%
Gene Interaction Network
Click a node to explore
NDUFAF8TMEM186NDUFAF3TIMMDC1NDUFAF7FOXRED1TMEM126B
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted Β· UniProt A1L188
View on AlphaFold β†—
Constraintβ“˜
LOEUFβ“˜
1.82LoF Tolerant
pLIβ“˜
0.00Tolerant
Observed/Expected LoF1.18 [0.72–1.82]
RankingsWhere NDUFAF8 stands among ~20K protein-coding genes
  • #17,114of 20,598
    Most Researched10
  • #3,652of 5,498
    Most Pathogenic Variants5
  • #16,693of 17,882
    Most Constrained (LOEUF)1.82
Genes detectedNDUFAF8
Sources retrieved4 papers
Response timeβ€”
πŸ“„ Sources
4
1
Recessive variants in mitochondrial Complex I nuclear subunits are an underrated cause of optic atrophy.
PMID: 41234160
Brain Β· 2025
1.00
2
Mitochondrial DNA or Genomic DNA Variant(s): Utility of Exhaustive Sequencing in Leigh Syndrome.
PMID: 39921456
Am J Med Genet A Β· 2025
0.75
3
Characterization of a Familial Goldenhar Syndrome Case Using Whole-Exome Sequencing.
PMID: 41898833
Genes (Basel) Β· 2026
0.50
4
Pathogenic Bi-allelic Mutations in NDUFAF8 Cause Leigh Syndrome with an Isolated Complex I Deficiency.
PMID: 31866046
Am J Hum Genet Β· 2020
0.25