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GeneE
10 sources retrieved Β· Most recent: April 2026 Β· Index updated 14 days ago
β“˜GeneE is for informational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment.
PDZD7
PDZ domain containing 7
Chromosome 10 Β· 10q24.31
NCBI Gene: 79955Ensembl: ENSG00000186862.20HGNC: HGNC:26257UniProt: A0A2R8Y892
31PubMed Papers
23Diseases
0Drugs
102Pathogenic Variants
RESEARCH IMPACT
Variant-Rich
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
nucleusciliumprotein bindingGO:0005615hearing loss, autosomal recessive 57Usher syndrome type 2Usher syndromeUsher syndrome type 2A
✦AI Summary

PDZD7 is a PDZ domain-containing scaffold protein essential for inner ear hair cell development and function through its role in organizing the ankle-link complex (ALC) at stereocilia 1. The protein contains three PDZ domains and a harmonin homology domain (HHD) that mediates membrane targeting 2. PDZD7 specifically localizes to the ankle region of developing stereocilia, where it forms the ALC together with USH2A, WHRN, and ADGRV1 through liquid-liquid phase separation 3. The long isoform of PDZD7 is specifically required for proper ankle-link formation and stereocilia development, as deletion of this isoform in mice causes stereocilia disorganization, reduced mechanotransduction currents, and hearing loss 1. PDZD7 also regulates USH2A protein stability by blocking adenylate cyclase inhibition mediated by ADGRV1, which affects cAMP-PKA signaling and subsequent WHRN phosphorylation 4. Mutations in PDZD7 contribute to Usher syndrome through digenic inheritance, acting as a modifier of retinal disease severity when combined with mutations in other Usher syndrome genes like USH2A and GPR98 5. The protein is associated with autosomal recessive deafness (DFNB57) and Usher syndrome types 2A and 2C, highlighting its clinical significance in hereditary hearing and vision disorders.

Sources cited
1
PDZD7 long isoform localizes at ankle region of stereocilia and is essential for ankle-link complex formation and hearing
PMID: 31914662
2
PDZD7 forms ankle-link complex with USH2A, WHRN, and ADGRV1 through liquid-liquid phase separation
PMID: 36964137
3
PDZD7 contains harmonin homology domain that mediates membrane targeting
PMID: 33937240
4
PDZD7 regulates USH2A stability through cAMP-PKA signaling and WHRN phosphorylation
PMID: 37066759
5
PDZD7 mutations contribute to digenic Usher syndrome and act as modifier of retinal disease severity
PMID: 20440071
6
PDZD7 is associated with Usher syndrome molecular diagnosis
PMID: 25404053
Disease Associationsβ“˜23
hearing loss, autosomal recessive 57Open Targets
0.74Strong
Usher syndrome type 2Open Targets
0.63Moderate
Usher syndromeOpen Targets
0.61Moderate
Usher syndrome type 2AOpen Targets
0.56Moderate
hearing loss, autosomal recessiveOpen Targets
0.54Moderate
deafnessOpen Targets
0.50Moderate
Hearing impairmentOpen Targets
0.46Moderate
genetic disorderOpen Targets
0.41Moderate
Retinal dystrophyOpen Targets
0.40Weak
autosomal dominant nonsyndromic hearing lossOpen Targets
0.29Weak
Rare genetic deafnessOpen Targets
0.28Weak
Abnormality of the earOpen Targets
0.27Weak
ear malformationOpen Targets
0.27Weak
nonsyndromic genetic hearing lossOpen Targets
0.27Weak
hepatocellular carcinomaOpen Targets
0.08Suggestive
X-linked nonsyndromic hearing lossOpen Targets
0.07Suggestive
autosomal dominant nonsyndromic hearing loss 17Open Targets
0.07Suggestive
autosomal dominant nonsyndromic hearing loss 7Open Targets
0.07Suggestive
deafness, aminoglycoside-inducedOpen Targets
0.07Suggestive
Mitochondrial non-syndromic sensorineural deafness with susceptibility to aminoglycoside exposureOpen Targets
0.07Suggestive
Deafness, autosomal recessive, 57UniProt
Usher syndrome 2AUniProt
Usher syndrome 2CUniProt
Pathogenic Variants102
NM_001195263.2(PDZD7):c.2089del (p.Ala697fs)Pathogenic
Hearing loss, autosomal recessive 57|not provided|Inborn genetic diseases|Autosomal recessive PDZD7-related disorders
β˜…β˜…β˜†β˜†2026β†’ Residue 697
NM_001195263.2(PDZD7):c.307G>C (p.Gly103Arg)Pathogenic
Hearing loss, autosomal recessive 57|not provided|Usher syndrome type 2C
β˜…β˜…β˜†β˜†2025β†’ Residue 103
NM_001195263.2(PDZD7):c.1933+1G>APathogenic
not provided|Hearing impairment|Hearing loss, autosomal recessive 57
β˜…β˜…β˜†β˜†2025
NM_001195263.2(PDZD7):c.1011C>G (p.Tyr337Ter)Pathogenic
not provided|PDZD7-related disorder
β˜…β˜…β˜†β˜†2025β†’ Residue 337
NM_001195263.2(PDZD7):c.2692dup (p.Ala898fs)Pathogenic
not provided
β˜…β˜…β˜†β˜†2025β†’ Residue 898
NM_001195263.2(PDZD7):c.2209_2211delinsAA (p.Gln737fs)Pathogenic
Deafness|not provided
β˜…β˜…β˜†β˜†2025β†’ Residue 737
NM_001195263.2(PDZD7):c.1750-2A>GLikely pathogenic
not provided|Hearing loss, autosomal recessive 57
β˜…β˜…β˜†β˜†2025
NM_001195263.2(PDZD7):c.928+1G>ALikely pathogenic
not provided|Hearing loss, autosomal recessive 57
β˜…β˜…β˜†β˜†2025
NM_001195263.2(PDZD7):c.2618-6_2619delLikely pathogenic
not provided
β˜…β˜…β˜†β˜†2025
NM_001195263.2(PDZD7):c.166dup (p.Arg56fs)Pathogenic
Usher syndrome type 2A|Hearing loss, autosomal recessive 57|not provided|Hearing loss, autosomal recessive|Usher syndrome type 2C
β˜…β˜…β˜†β˜†2025β†’ Residue 56
NM_001195263.2(PDZD7):c.2211del (p.Gln737fs)Pathogenic
Nonsyndromic genetic hearing loss|Hearing loss, autosomal recessive
β˜…β˜…β˜†β˜†2024β†’ Residue 737
NM_001195263.2(PDZD7):c.918dup (p.Leu307fs)Pathogenic
not provided|Hearing loss, autosomal recessive 57
β˜…β˜…β˜†β˜†2023β†’ Residue 307
NM_001195263.2(PDZD7):c.1113del (p.Thr372fs)Pathogenic
not provided
β˜…β˜…β˜†β˜†2023β†’ Residue 372
NM_001195263.2(PDZD7):c.1655dup (p.Ala553fs)Pathogenic
not provided|PDZD7-related disorder
β˜…β˜…β˜†β˜†2023β†’ Residue 553
NM_001195263.2(PDZD7):c.1543C>T (p.Gln515Ter)Pathogenic
not provided|Usher syndrome type 2C|Hearing loss, autosomal recessive 57
β˜…β˜…β˜†β˜†2023β†’ Residue 515
NM_001195263.2(PDZD7):c.1648C>T (p.Gln550Ter)Pathogenic
Hearing loss, autosomal recessive 57|not provided
β˜…β˜…β˜†β˜†2023β†’ Residue 550
NM_001195263.2(PDZD7):c.1012del (p.Ser338fs)Pathogenic
Usher syndrome type 2A|not provided
β˜…β˜…β˜†β˜†2023β†’ Residue 338
NM_001195263.2(PDZD7):c.993C>A (p.Cys331Ter)Pathogenic
not provided
β˜…β˜…β˜†β˜†2023β†’ Residue 331
NM_001195263.2(PDZD7):c.854T>G (p.Met285Arg)Likely pathogenic
Hearing loss, autosomal recessive 57
β˜…β˜…β˜†β˜†2018β†’ Residue 285
NM_001195263.2(PDZD7):c.121C>T (p.Arg41Ter)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 41
View on ClinVar β†—
Related Genes
USH1GProtein interaction100%MYO7AProtein interaction92%CLRN1Protein interaction92%USH1CProtein interaction92%CIB2Protein interaction92%MYO15AProtein interaction92%
Tissue Expression6 tissues
Brain
100%
Bone Marrow
46%
Ovary
34%
Heart
14%
Lung
13%
Liver
8%
Gene Interaction Network
Click a node to explore
PDZD7USH1GMYO7ACLRN1USH1CCIB2MYO15A
PROTEIN STRUCTURE
Preparing viewer…
PDB7PC5 Β· 1.70 Γ… Β· X-ray
View on RCSB β†—
Constraintβ“˜
LOEUFβ“˜
1.06LoF Tolerant
pLIβ“˜
0.00Tolerant
Observed/Expected LoF0.87 [0.72–1.06]
RankingsWhere PDZD7 stands among ~20K protein-coding genes
  • #11,770of 20,598
    Most Researched31
  • #762of 5,498
    Most Pathogenic Variants102 Β· top quartile
  • #10,616of 17,882
    Most Constrained (LOEUF)1.06
Genes detectedPDZD7
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
Targeted next generation sequencing for molecular diagnosis of Usher syndrome.
PMID: 25404053
Orphanet J Rare Dis Β· 2014
1.00
2
Temporal and spatial assembly of inner ear hair cell ankle link condensate through phase separation.
PMID: 36964137
Nat Commun Β· 2023
0.90
3
Deafness-Associated ADGRV1 Mutation Impairs USH2A Stability through Improper Phosphorylation of WHRN and WDSUB1 Recruitment.
PMID: 37066759
Adv Sci (Weinh) Β· 2023
0.80
4
Lack of PDZD7 long isoform disrupts ankle-link complex and causes hearing loss in mice.
PMID: 31914662
FASEB J Β· 2020
0.70
5
Deafness-related protein PDZD7 forms complex with the C-terminal tail of FCHSD2.
PMID: 35695292
Biochem J Β· 2022
0.60