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GeneE
10 sources retrieved Β· Most recent: April 2026 Β· Index updated 14 days ago
β“˜GeneE is for informational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment.
PIGL
phosphatidylinositol glycan anchor biosynthesis class L
Chromosome 17 Β· 17p11.2
NCBI Gene: 9487Ensembl: ENSG00000108474.17HGNC: HGNC:8966UniProt: A8MTV0
19PubMed Papers
21Diseases
0Drugs
20Pathogenic Variants
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
GPI anchor biosynthetic processendoplasmic reticulum membraneN-acetylglucosaminylphosphatidylinositol deacetylase activityendoplasmic reticulumCHIME syndromesyndromic intellectual disabilityhyperphosphatasia-intellectual disability syndromegenetic disorder
✦AI Summary

PIGL encodes a key enzyme in glycosylphosphatidylinositol (GPI) anchor biosynthesis, catalyzing the de-N-acetylation of N-acetylglucosaminyl-phosphatidylinositol in the endoplasmic reticulum. Beyond its canonical metabolic role, PIGL exhibits dual subcellular localization with distinct functions: cytoplasmic PIGL participates in GPI biosynthesis, while nuclear PIGL acts as a tumor suppressor by disrupting the cMyc/BRD4 transcriptional axis, reducing expression of immunosuppressive chemokines CCL2 and CCL20 1. PIGL phosphorylation at Y81 by FGFR2 retains the protein in the cytosol, promoting tumor immune evasion 1. The protein is essential for placental development, particularly syncytiotrophoblast differentiation, and its deficiency triggers excessive unfolded protein response and impairs WNT signaling 2. PIGL mutations cause two distinct autosomal recessive disorders: CHIME syndrome (colobomas, heart defects, ichthyosiform dermatosis, intellectual disability, ear anomalies) and Mabry syndrome (hyperphosphatasia with mental retardation syndrome) 3 4. The gene's high Alu repeat content (~34% of intronic sequence) predisposes it to deletion mutations 5. Recent genome-wide association studies have also identified PIGL as a potential novel risk locus for Parkinson's disease 6.

Sources cited
1
Nuclear PIGL disrupts cMyc/BRD4 interaction, reduces CCL2/CCL20 expression, and FGFR2 phosphorylation at Y81 affects subcellular localization
PMID: 37280393
2
PIGL is critical for syncytiotrophoblast differentiation and placental development, with deficiency causing UPR and impaired WNT signaling
PMID: 38819479
3
PIGL mutations cause CHIME syndrome with features including congenital diaphragmatic hernia and early lethality
PMID: 35378319
4
PIGL mutations cause Mabry syndrome (HPMRS) with developmental delay, cognitive impairment, and high alkaline phosphatase
PMID: 30023290
5
PIGL has high Alu repeat content (~34% intronic sequence) predisposing to deletion mutations
PMID: 28371479
6
PIGL identified as potential novel risk locus for Parkinson's disease in multi-ancestry GWAS
PMID: 38155330
Disease Associationsβ“˜21
CHIME syndromeOpen Targets
0.80Strong
syndromic intellectual disabilityOpen Targets
0.45Moderate
hyperphosphatasia-intellectual disability syndromeOpen Targets
0.44Moderate
genetic disorderOpen Targets
0.41Moderate
Intellectual disabilityOpen Targets
0.34Weak
diabetic ketoacidosisOpen Targets
0.20Weak
protozoa infectious diseaseOpen Targets
0.19Weak
risk-taking behaviourOpen Targets
0.14Weak
smoking initiationOpen Targets
0.13Weak
Hodgkins lymphomaOpen Targets
0.13Weak
camptodactyly of fingersOpen Targets
0.12Weak
cleft lipOpen Targets
0.12Weak
HypertelorismOpen Targets
0.12Weak
Low-set earsOpen Targets
0.12Weak
Postaxial hand polydactylyOpen Targets
0.12Weak
premature birthOpen Targets
0.12Weak
Wide intermamillary distanceOpen Targets
0.12Weak
asthmaOpen Targets
0.11Weak
response to stimulusOpen Targets
0.09Suggestive
mathematical abilityOpen Targets
0.05Suggestive
Coloboma, congenital heart disease, ichthyosiform dermatosis, impaired intellectual development, and ear anomalies syndromeUniProt
Pathogenic Variants20
NM_004278.4(PIGL):c.500T>C (p.Leu167Pro)Pathogenic
CHIME syndrome|not provided|8 conditions|PIGL-related disorder|Inborn genetic diseases|Intellectual disability
β˜…β˜…β˜†β˜†2026β†’ Residue 167
NM_004278.4(PIGL):c.701G>A (p.Arg234His)Pathogenic
not provided
β˜…β˜…β˜†β˜†2024β†’ Residue 234
NM_004278.4(PIGL):c.427-1G>APathogenic
CHIME syndrome|not provided|Syndromic intellectual disability
β˜…β˜…β˜†β˜†2024
NM_004278.4(PIGL):c.336-2A>GPathogenic
not provided
β˜…β˜…β˜†β˜†2023
NM_004278.4(PIGL):c.236-4664_335+2566delLikely pathogenic
CHIME syndrome
β˜…β˜†β˜†β˜†2025
NM_004278.4(PIGL):c.115_155del (p.Gly38_Ala39insTer)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 38
NM_004278.4(PIGL):c.26_27del (p.Val9fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 9
NM_004278.4(PIGL):c.391del (p.Leu131fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2024β†’ Residue 131
NM_004278.4(PIGL):c.438C>A (p.Phe146Leu)Likely pathogenic
CHIME syndrome;Hyperphosphatasia with intellectual disability syndrome 1|PIGL-related disorder|not provided
β˜…β˜†β˜†β˜†2023β†’ Residue 146
NM_004278.4(PIGL):c.271del (p.Glu91fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2022β†’ Residue 91
NM_004278.4(PIGL):c.154_161del (p.Asp52fs)Likely pathogenic
CHIME syndrome
β˜…β˜†β˜†β˜†2022β†’ Residue 52
NM_004278.4(PIGL):c.660+1G>TLikely pathogenic
CHIME syndrome
β˜…β˜†β˜†β˜†2022
NM_004278.4(PIGL):c.262C>T (p.Arg88Cys)Likely pathogenic
not provided
β˜…β˜†β˜†β˜†2020β†’ Residue 88
NM_004278.4(PIGL):c.60G>A (p.Trp20Ter)Pathogenic
not provided
β˜…β˜†β˜†β˜†2020β†’ Residue 20
NM_004278.4(PIGL):c.494+1G>ALikely pathogenic
CHIME syndrome
β˜…β˜†β˜†β˜†2019
NM_004278.4(PIGL):c.660+1G>ALikely pathogenic
not provided
β˜…β˜†β˜†β˜†2016
NM_004278.4(PIGL):c.724del (p.Arg242fs)Likely pathogenic
not provided
β˜…β˜†β˜†β˜†2016β†’ Residue 242
NM_004278.4(PIGL):c.154G>A (p.Asp52Asn)Likely pathogenic
not provided
β˜†β˜†β˜†β˜†2019β†’ Residue 52
NM_004278.4(PIGL):c.652C>T (p.Gln218Ter)Pathogenic
CHIME syndrome
β˜†β˜†β˜†β˜†2012β†’ Residue 218
NM_004278.4(PIGL):c.274del (p.Leu92fs)Pathogenic
CHIME syndrome
β˜†β˜†β˜†β˜†2012β†’ Residue 92
View on ClinVar β†—
Related Genes
PGAP4Shared pathway100%PIGZShared pathway100%CWH43Shared pathway100%PIGXShared pathway100%PIGPProtein interaction100%PIGYProtein interaction100%
Tissue Expression6 tissues
Liver
100%
Ovary
100%
Bone Marrow
78%
Lung
67%
Heart
39%
Brain
26%
Gene Interaction Network
Click a node to explore
PIGLPGAP4PIGZCWH43PIGXPIGPPIGY
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted Β· UniProt Q9Y2B2
View on AlphaFold β†—
Constraintβ“˜
LOEUFβ“˜
1.24LoF Tolerant
pLIβ“˜
0.00Tolerant
Observed/Expected LoF0.79 [0.52–1.24]
RankingsWhere PIGL stands among ~20K protein-coding genes
  • #14,491of 20,598
    Most Researched19
  • #2,209of 5,498
    Most Pathogenic Variants20
  • #13,072of 17,882
    Most Constrained (LOEUF)1.24
Genes detectedPIGL
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
Multi-ancestry genome-wide association meta-analysis of Parkinson's disease.
PMID: 38155330
Nat Genet Β· 2024
1.00
2
Metabolic Cardiomyopathies and Cardiac Defects in Inherited Disorders of Carbohydrate Metabolism: A Systematic Review.
PMID: 37239976
Int J Mol Sci Β· 2023
0.90
3
Elevated nuclear PIGL disrupts the cMyc/BRD4 axis and improves PD-1 blockade therapy by dampening tumor immune evasion.
PMID: 37280393
Cell Mol Immunol Β· 2023
0.80
4
The GPI-anchor biosynthesis pathway is critical for syncytiotrophoblast differentiation and placental development.
PMID: 38819479
Cell Mol Life Sci Β· 2024
0.70
5
Congenital diaphragmatic hernia and early lethality in PIGL-related disorder.
PMID: 35378319
Eur J Med Genet Β· 2022
0.60