HomeAboutRankingsData Sources
Β© 2026 GeneE
🧬
GeneE
10 sources retrieved Β· Most recent: April 2026 Β· Index updated 15 days ago
β“˜GeneE is for informational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment.
ARL2BP
ARF like GTPase 2 binding protein
Chromosome 16 Β· 16q13
NCBI Gene: 23568Ensembl: ENSG00000102931.8HGNC: HGNC:17146UniProt: Q9Y2Y0
43PubMed Papers
21Diseases
0Drugs
16Pathogenic Variants
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
transcription coactivator activityprotein bindingpositive regulation of tyrosine phosphorylation of STAT proteinmaintenance of protein location in nucleusretinitis pigmentosa with or without situs inversusretinitis pigmentosaRetinal dystrophyautosomal recessive retinitis pigmentosa
✦AI Summary

ARL2BP (ARL2 binding protein) is a ciliary effector protein that functions as a regulator of primary cilia structure and photoreceptor maintenance. ARL2BP localizes to the basal body and cilium-associated structures of photoreceptors, where it works with the small GTPase ARL2 to maintain ciliary length and stability 1. The protein plays a critical role in ciliary microtubule organization and is essential for normal spermiogenesis and sperm flagellar assembly 2. Mutations in ARL2BP cause autosomal-recessive retinitis pigmentosa (RP66), characterized by progressive photoreceptor degeneration leading to visual failure 13. ARL2BP mutations account for approximately 0.1% of autosomal recessive rod-cone dystrophies 3. Beyond retinal disease, homozygous ARL2BP variants present as syndromic ciliopathies, including situs inversus totalis, male infertility with oligozoospermia or asthenozoospermia, and olfactory dysfunction 425. Disease-causing mutations impair ARL2BP localization at the basal body, reduce ARL2 binding, and result in cilia shortening and abnormal ciliogenesis 1. Recent findings expand the syndromic phenotype to include renal agenesis with microcysts 5, necessitating differential diagnosis with Senior-Loken and Bardet-Biedl syndromes in patients presenting with retinal dystrophy and renal abnormalities.

Sources cited
1
ARL2BP is an effector protein of ARL2 and ARL3; mutations cause autosomal-recessive RP; ARL2BP localizes to basal body and cilium; depletion causes cilia shortening; ARL2 is vital for ARL2BP recruitment at the basal body
PMID: 23849777
2
Homozygous ARL2BP variant causes RP, situs inversus totalis, oligozoospermia, and olfactory dysfunction; ciliary gene associated with ciliopathy; reduced fibroblast proliferation and ciliary length
PMID: 36507858
3
ARL2BP is required for ciliary microtubule structure and sperm flagellar assembly; mutations cause spermiogenesis impairment with abnormal sperm heads and tails; loss of axonemal doublets; syndromic ciliopathy phenotypes
PMID: 31425546
4
ARL2BP mutations account for 0.1% of autosomal recessive rod-cone dystrophies
PMID: 27790702
5
Homozygous ARL2BP splice variant causes syndromic rod-cone dystrophy with situs inversus, asthenozoospermia, unilateral renal agenesis and microcysts; expands clinical manifestations of ARL2BP variants
PMID: 38649918
6
Homozygous splice site variants in ARL2BP identified as rare cause of autosomal recessive RP; variants alter pre-mRNA splicing
PMID: 30210231
Disease Associationsβ“˜21
retinitis pigmentosa with or without situs inversusOpen Targets
0.68Moderate
retinitis pigmentosaOpen Targets
0.62Moderate
Retinal dystrophyOpen Targets
0.44Moderate
autosomal recessive retinitis pigmentosaOpen Targets
0.42Moderate
ciliopathyOpen Targets
0.37Weak
genetic disorderOpen Targets
0.19Weak
nasopharyngeal carcinomaOpen Targets
0.09Suggestive
azoospermiaOpen Targets
0.09Suggestive
neoplasmOpen Targets
0.08Suggestive
partial chromosome Y deletionOpen Targets
0.06Suggestive
spermatogenic failure 65Open Targets
0.06Suggestive
spermatogenic failure 84Open Targets
0.06Suggestive
spermatogenic failure 93Open Targets
0.06Suggestive
spermatogenic failure 78Open Targets
0.06Suggestive
spermatogenic failure 56Open Targets
0.06Suggestive
spermatogenic failure 92Open Targets
0.06Suggestive
spermatogenic failure 94Open Targets
0.06Suggestive
spermatogenic failure 54Open Targets
0.06Suggestive
spermatogenic failure, X-linked, 3Open Targets
0.06Suggestive
spermatogenic failure 72Open Targets
0.06Suggestive
Retinitis pigmentosa 82 with or without situs inversusUniProt
Pathogenic Variants16
NM_012106.4(ARL2BP):c.207+1G>APathogenic
Retinal dystrophy|not provided|ARL2BP-related disorder|Retinitis pigmentosa with or without situs inversus|Cholangiocarcinoma
β˜…β˜…β˜†β˜†2025
NM_012106.4(ARL2BP):c.293+5G>ALikely pathogenic
Retinitis pigmentosa with or without situs inversus|not provided
β˜…β˜…β˜†β˜†2023
NM_012106.4(ARL2BP):c.191del (p.Pro64fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2024β†’ Residue 64
NM_012106.4(ARL2BP):c.207C>A (p.Tyr69Ter)Pathogenic
not provided
β˜…β˜†β˜†β˜†2023β†’ Residue 69
NM_012106.4(ARL2BP):c.37_38del (p.Phe13fs)Pathogenic
Retinal dystrophy
β˜…β˜†β˜†β˜†2023β†’ Residue 13
NM_012106.4(ARL2BP):c.39-1G>CLikely pathogenic
not provided
β˜…β˜†β˜†β˜†2023
NM_012106.4(ARL2BP):c.294-17_342delLikely pathogenic
not provided
β˜…β˜†β˜†β˜†2023
NM_012106.4(ARL2BP):c.33_36del (p.Phe13fs)Pathogenic
Retinitis pigmentosa|Retinitis pigmentosa with or without situs inversus
β˜…β˜†β˜†β˜†2023β†’ Residue 13
NM_012106.4(ARL2BP):c.235G>T (p.Glu79Ter)Pathogenic
not provided
β˜…β˜†β˜†β˜†2023β†’ Residue 79
NM_012106.4(ARL2BP):c.97_98dup (p.Met33fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2022β†’ Residue 33
NM_012106.4(ARL2BP):c.139_143dup (p.Tyr48Ter)Pathogenic
not provided
β˜…β˜†β˜†β˜†2021β†’ Residue 48
NM_012106.4(ARL2BP):c.22_23del (p.Ser8fs)Pathogenic
Retinitis pigmentosa with or without situs inversus
β˜†β˜†β˜†β˜†2024β†’ Residue 8
NM_012106.4(ARL2BP):c.294-1G>CPathogenic
Retinitis pigmentosa with or without situs inversus
β˜†β˜†β˜†β˜†2024
NM_012106.4(ARL2BP):c.101-1G>CPathogenic
Retinitis pigmentosa with or without situs inversus|Retinitis pigmentosa|Autosomal recessive retinitis pigmentosa
β˜†β˜†β˜†β˜†2019
NM_012106.4(ARL2BP):c.38+2T>GPathogenic
Retinitis pigmentosa
β˜†β˜†β˜†β˜†2019
NM_012106.4(ARL2BP):c.207+1G>TPathogenic
Retinitis pigmentosa with or without situs inversus|Autosomal recessive retinitis pigmentosa
β˜†β˜†β˜†β˜†2018
View on ClinVar β†—
Related Genes
ARL2Protein interaction100%CFAP20Protein interaction85%ARL3Protein interaction83%SUPT7LShared pathway25%PARP14Shared pathway17%TNFRSF18Shared pathway17%
Tissue Expression6 tissues
Brain
100%
Ovary
10%
Lung
10%
Heart
9%
Liver
4%
Bone Marrow
2%
Gene Interaction Network
Click a node to explore
ARL2BPARL2CFAP20ARL3SUPT7LPARP14TNFRSF18
PROTEIN STRUCTURE
Preparing viewer…
PDB3DOE Β· 2.25 Γ… Β· X-ray
View on RCSB β†—
Constraintβ“˜
LOEUFβ“˜
1.03LoF Tolerant
pLIβ“˜
0.01Tolerant
Observed/Expected LoF0.61 [0.37–1.03]
RankingsWhere ARL2BP stands among ~20K protein-coding genes
  • #9,690of 20,598
    Most Researched43
  • #2,417of 5,498
    Most Pathogenic Variants16
  • #10,194of 17,882
    Most Constrained (LOEUF)1.03
Genes detectedARL2BP
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
PMID: 20301590
1.00
2
Novel homozygous variant in ARL2BP associated with retinitis pigmentosa, situs inversus, and male infertility in a Chinese patient.
PMID: 36507858
Clin Genet Β· 2023
0.90
3
Mutations in ARL2BP, encoding ADP-ribosylation-factor-like 2 binding protein, cause autosomal-recessive retinitis pigmentosa.
PMID: 23849777
Am J Hum Genet Β· 2013
0.80
4
Novel homozygous splicing mutations in
PMID: 30210231
Mol Vis Β· 2018
0.70
5
Mutations in ARL2BP, a protein required for ciliary microtubule structure, cause syndromic male infertility in humans and mice.
PMID: 31425546
PLoS Genet Β· 2019
0.60