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10 sources retrieved Β· Most recent: April 2026 Β· Index updated 15 days ago
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ATXN10
ataxin 10
Chromosome 22 Β· 22q13.31
NCBI Gene: 25814Ensembl: ENSG00000130638.18HGNC: HGNC:10549UniProt: Q9UBB4
145PubMed Papers
21Diseases
0Drugs
4Pathogenic Variants
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
dendritemidbodyneuron projection developmentregulation of cytokinesisspinocerebellar ataxia type 10neurodegenerative diseaseDupuytren Contractureinvasive mechanical ventilation
✦AI Summary

ATXN10 encodes ataxin-10, a protein primarily involved in regulating cytokinesis and neuronal development 12. The protein localizes to perinuclear cytoplasmic regions, the midbody, and dendrites, where it functions in neuritogenesis by activating the Ras-MAP kinase pathway and supporting cerebellar neuron survival [UniProt]. ATXN10 also binds ataxia-associated proteins and localizes to stress granules, potentially modulating protein glycosylation and cellular signaling 3. Pathogenic ATTCT pentanucleotide repeat expansions in ATXN10 intron 9 cause spinocerebellar ataxia type 10 (SCA10), an autosomal dominant neurodegenerative disorder 45. SCA10 presents with progressive cerebellar ataxia, with variable phenotypes including epilepsy, particularly in Mexican and some Brazilian populations, though epilepsy-free presentations occur in other regions 65. Notably, uninterrupted repeat expansions (ATTCTint+) associate with earlier disease onset, higher seizure frequency, and worse clinical severity compared to interrupted repeats (ATTCTint-) 7. While ATXN10 expansions account for significant hereditary cerebellar ataxia cases in the Americas, standard whole-genome sequencing struggles with accurate repeat sizing 8.

Sources cited
1
ATXN10 plays a role in regulating cytokinesis
PMID: 21857149
2
ATXN10 plays a role in regulating cytokinesis
PMID: 25666058
3
PEG10 binds to ataxia-associated proteins including ATXN10 and localizes to stress granules
PMID: 34467244
4
SCA10 is caused by ATTCT repeat expansion in ATXN10 intron 9; ATTCT repeats originated in hominoids through retrotransposon-mediated mechanisms
PMID: 19651850
5
SCA10 is caused by ATTCT pentanucleotide repeat expansion in ATXN10 intron 9; predominant in Indigenous American and East Asian populations with regional phenotypic variation
PMID: 40232546
6
19.6% of ataxia patients showed ATXN10 expansions; SCA10 can present with ataxia without epilepsy, challenging previous diagnostic assumptions
PMID: 39820777
7
Uninterrupted ATTCT repeats (ATTCTint+) associate with earlier age of onset, higher seizure frequency, and worse ataxia severity compared to interrupted repeats (ATTCTint-)
PMID: 40067487
8
ATXN10 repeat expansions account for significant hereditary cerebellar ataxia cases; whole-genome sequencing has limitations in detecting and sizing large repeat expansions
PMID: 40488180
Disease Associationsβ“˜21
spinocerebellar ataxia type 10Open Targets
0.65Moderate
neurodegenerative diseaseOpen Targets
0.44Moderate
Dupuytren ContractureOpen Targets
0.27Weak
invasive mechanical ventilationOpen Targets
0.26Weak
benign endocrine neoplasmOpen Targets
0.26Weak
benign neoplasm of adrenal glandOpen Targets
0.26Weak
ulcerative colitisOpen Targets
0.25Weak
genetic disorderOpen Targets
0.18Weak
Malignant Laryngeal NeoplasmOpen Targets
0.11Weak
musculoskeletal system diseaseOpen Targets
0.10Weak
sleep apneaOpen Targets
0.10Suggestive
metabolic diseaseOpen Targets
0.06Suggestive
gastroesophageal reflux diseaseOpen Targets
0.05Suggestive
cancerOpen Targets
0.04Suggestive
benign prostatic hyperplasiaOpen Targets
0.04Suggestive
CachexiaOpen Targets
0.02Suggestive
autosomal dominant cerebellar ataxiaOpen Targets
0.02Suggestive
thrombophiliaOpen Targets
0.02Suggestive
Parkinson diseaseOpen Targets
0.02Suggestive
cerebellar ataxiaOpen Targets
0.01Suggestive
Spinocerebellar ataxia 10UniProt
Pathogenic Variants4
NM_013236.3(ATXN10):c.1173+54822_1173+54826ATTCT(360_370)Pathogenic
Spinocerebellar ataxia type 10
β˜†β˜†β˜†β˜†2012
NM_013236.3(ATXN10):c.1173+54822_1173+54826ATTCT(400_760)Pathogenic
Spinocerebellar ataxia type 10
β˜†β˜†β˜†β˜†2012
NM_013236.3(ATXN10):c.1173+54822_1173+54826ATTCT(800_4500)Pathogenic
Spinocerebellar ataxia type 10
β˜†β˜†β˜†β˜†2012
NM_013236.3(ATXN10):c.1173+54822_1173+54826ATTCT[850]Pathogenic
Spinocerebellar ataxia type 10
β˜†β˜†β˜†β˜†2012
View on ClinVar β†—
Related Genes
SPTBN2Protein interaction92%CACNA1AProtein interaction90%ATXN7Protein interaction86%TTBK2Protein interaction84%IQCB1Protein interaction81%PPP2R2BProtein interaction81%
Tissue Expression6 tissues
Brain
100%
Heart
84%
Ovary
49%
Bone Marrow
43%
Liver
42%
Lung
35%
Gene Interaction Network
Click a node to explore
ATXN10SPTBN2CACNA1AATXN7TTBK2IQCB1PPP2R2B
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted Β· UniProt Q9UBB4
View on AlphaFold β†—
Constraintβ“˜
LOEUFβ“˜
0.72LoF Tolerant
pLIβ“˜
0.00Tolerant
Observed/Expected LoF0.52 [0.38–0.72]
RankingsWhere ATXN10 stands among ~20K protein-coding genes
  • #3,127of 20,598
    Most Researched145 Β· top quartile
  • #3,717of 5,498
    Most Pathogenic Variants4
  • #5,535of 17,882
    Most Constrained (LOEUF)0.72
Genes detectedATXN10
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
Alu-mediated acquisition of unstable ATTCT pentanucleotide repeats in the human ATXN10 gene.
PMID: 19651850
Mol Biol Evol Β· 2009
1.00
2
Secreted retrovirus-like GAG-domain-containing protein PEG10 is regulated by UBE3A and is involved in Angelman syndrome pathophysiology.
PMID: 34467244
Cell Rep Med Β· 2021
0.90
3
ATXN10 Gene Expansions in Mexican Patients with Ataxia Without Epilepsy.
PMID: 39820777
Cerebellum Β· 2025
0.80
4
Spinocerebellar Ataxia Type 10 (SCA 10) in Brazil.
PMID: 40232546
Cerebellum Β· 2025
0.70
5
A FEMALE CASE OF SPINOCEREBELLAR ATAXIA TYPE 10 WITH SUICIDAL BEHAVIOR AND ENDOCRINPATHIES ASSOCIATED WITH A MASSIVE EXPANSION (ATTCT) OF THE GENE ATXN10.
PMID: 35103298
Actas Esp Psiquiatr Β· 2022
0.60