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10 sources retrieved · Most recent: April 2026 · Index updated 14 days ago
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GPATCH1
G-patch domain containing 1
Chromosome 19 · 19q13.11
NCBI Gene: 55094Ensembl: ENSG00000076650.8HGNC: HGNC:24658UniProt: Q9BRR8
53PubMed Papers
20Diseases
0Drugs
0Pathogenic Variants
DATA QUALITY
✓ Experimental GO Evidence✓ Swiss-Prot Reviewed
catalytic step 2 spliceosomenucleusRNA bindingnucleoplasmneurodegenerative diseasecolorectal canceropen-angle glaucomathrombophilia
✦AI Summary

GPATCH1 (G-patch domain containing 1) is a conserved spliceosomal protein that functions as a splicing fidelity factor. It localizes to the nucleus and nucleoplasm where it participates in catalytic step 2 of the spliceosome 1. GPATCH1 functions as part of a conserved G-patch/helicase pair with DHX35 (human homolog of yeast Gih35), working together to promote splicing accuracy and suppress cryptic splice site usage 2. Structurally, GPATCH1 recognizes remodeled spliceosomal active sites and helps maintain catalytic dormancy during quality control surveillance 1. The protein interacts with host splicing machinery and can be competitively bound by viral factors; HTLV-1 Tax protein inhibits HBZ gene splicing by competing for GPATCH1 binding 3. Clinically, GPATCH1 variants are associated with multiple disease phenotypes. Genome-wide association studies identified GPATCH1 as a novel candidate gene for congenital heart disease (CHD), with mutations enriched in CHD patients 4. Additionally, SNPs in GPATCH1 (rs10416265) show significant associations with osteoporosis susceptibility and fracture risk in multiple populations 5 6. GPATCH1 appears to function as a tissue-specific splicing factor 7, suggesting its effects on bone metabolism and cardiac development may involve splicing regulation of lineage-specific genes.

Sources cited
1
GPATCH1 recognizes remodeled spliceosomal active sites and maintains catalytic dormancy during splicing quality control as part of a DEAH-box helicase-G-patch protein pair
PMID: 39833470
2
GPATCH1 ortholog functions as a conserved G-patch/helicase pair with DHX35 to promote splicing fidelity and suppress cryptic splice site usage
PMID: 34555349
3
GPATCH1 is a host splicing factor that can be competitively bound by HTLV-1 Tax to inhibit HBZ gene splicing
PMID: 40720552
4
GPATCH1 is identified as a novel candidate gene for congenital heart disease through variant enrichment analysis in CHD cases
PMID: 37811720
5
GPATCH1 SNP rs10416265 shows genome-wide significant association with heel bone properties and osteoporosis susceptibility
PMID: 24430505
6
GPATCH1 rs10416265 minor allele is a risk allele for vertebral fracture in osteoporosis patients
PMID: 28580384
7
GPATCH1 functions as a tissue-specific splicing factor associated with human osteoporosis
PMID: 39607466
Disease Associationsⓘ20
neurodegenerative diseaseOpen Targets
0.50Moderate
colorectal cancerOpen Targets
0.37Weak
open-angle glaucomaOpen Targets
0.24Weak
thrombophiliaOpen Targets
0.23Weak
polyp of colonOpen Targets
0.22Weak
biliary tract diseaseOpen Targets
0.16Weak
orofacial cleftOpen Targets
0.15Weak
papillary adenocarcinomaOpen Targets
0.11Weak
rectum cancerOpen Targets
0.09Suggestive
colorectal adenocarcinomaOpen Targets
0.08Suggestive
malignant colon neoplasmOpen Targets
0.03Suggestive
alcohol drinkingOpen Targets
0.03Suggestive
Abnormality of the gastrointestinal tractOpen Targets
0.02Suggestive
cervical carcinomaOpen Targets
0.02Suggestive
osteoporosisOpen Targets
0.01Suggestive
influenzaOpen Targets
0.00Suggestive
invasive breast ductal carcinomaOpen Targets
0.00Suggestive
type 1 diabetes mellitusOpen Targets
0.00Suggestive
KeloidOpen Targets
0.00Suggestive
lung cancerOpen Targets
0.00Suggestive
Pathogenic Variants
No pathogenic variants reported on ClinVar for this gene.
View on ClinVar ↗
Related Genes
HNRNPRShared pathway100%WDR83Protein interaction91%PLRG1Protein interaction86%EAPPProtein interaction83%TSSC4Protein interaction80%USB1Protein interaction79%
Tissue Expression6 tissues
Brain
100%
Ovary
72%
Liver
56%
Lung
43%
Bone Marrow
42%
Heart
41%
Gene Interaction Network
Click a node to explore
GPATCH1HNRNPRWDR83PLRG1EAPPTSSC4USB1
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted · UniProt Q9BRR8
View on AlphaFold ↗
Constraintⓘ
LOEUFⓘ
0.72LoF Tolerant
pLIⓘ
0.00Tolerant
Observed/Expected LoF0.56 [0.43–0.72]
RankingsWhere GPATCH1 stands among ~20K protein-coding genes
  • #8,429of 20,598
    Most Researched53
  • #5,571of 17,882
    Most Constrained (LOEUF)0.72
Genes detectedGPATCH1
Sources retrieved10 papers
Response time—
📄 Sources
10▼
1
Structures of aberrant spliceosome intermediates on their way to disassembly.
PMID: 39833470
Nat Struct Mol Biol · 2025
1.00
2
Splicing-dependent restriction of the HBZ gene by Tax underlies biphasic HTLV-1 infection.
PMID: 40720552
PLoS Pathog · 2025
0.90
3
Single-cell reconstruction and mutation enrichment analysis identifies dysregulated cardiomyocyte and endothelial cells in congenital heart disease.
PMID: 37811720
Physiol Genomics · 2023
0.80
4
Coupling of spliceosome complexity to intron diversity.
PMID: 34555349
Curr Biol · 2021
0.70
5
Genetic determinants of heel bone properties: genome-wide association meta-analysis and replication in the GEFOS/GENOMOS consortium.
PMID: 24430505
Hum Mol Genet · 2014
0.60