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10 sources retrieved Β· Most recent: April 2026 Β· Index updated 15 days ago
β“˜GeneE is for informational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment.
NDUFA2
NADH:ubiquinone oxidoreductase subunit A2
Chromosome 5 Β· 5q31.3
NCBI Gene: 4695Ensembl: ENSG00000131495.9HGNC: HGNC:7685UniProt: O43678
68PubMed Papers
21Diseases
3Drugs
3Pathogenic Variants
FUNCTIONAL ROLE
Hub GeneTransporter
CLINICAL
FDA Approved TargetOMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
respiratory chain complex Imitochondrial inner membranemitochondrionmitochondrial membranemitochondrial complex I deficiencymitochondrial complex I deficiency, nuclear type 13type 2 diabetes mellitusdiabetes mellitus
✦AI Summary

NDUFA2 encodes an accessory subunit of mitochondrial respiratory chain Complex I (NADH:ubiquinone oxidoreductase), functioning in electron transfer from NADH to ubiquinone within the mitochondrial inner membrane 1. While considered non-catalytic, NDUFA2 is essential for proper Complex I assembly and activity 2. Mutations in NDUFA2 cause mitochondrial Complex I deficiency, manifesting as severe neurological phenotypes including cystic leukoencephalopathy and Leigh syndrome 12. A homozygous splice-site mutation results in exon 2 skipping, leading to reduced Complex I activity, disturbed assembly, and mitochondrial depolarization 2. Beyond primary mitochondrial disorders, NDUFA2 shows broader disease relevance. In myocardial infarction, NDUFA2 downregulation correlates with reduced cardiac function and altered immune infiltration patterns 3. Interestingly, decreased NDUFA2 expression in brain cortex associates with reduced Alzheimer's disease risk and favorable cognitive function, potentially through mitochondrial Complex I modulation 4. The gene also demonstrates prognostic significance in cervical squamous cell carcinoma 5 and shows differential regulation in ovarian cancer drug resistance 6. These findings highlight NDUFA2's critical role in mitochondrial function and its involvement in diverse pathological processes beyond classical mitochondrial diseases.

Sources cited
1
NDUFA2 is an accessory subunit of Complex I and mutations cause cystic leukoencephalopathy
PMID: 28857146
2
NDUFA2 mutations cause Leigh disease through disturbed Complex I assembly and mitochondrial depolarization
PMID: 18513682
3
NDUFA2 downregulation in myocardial infarction correlates with reduced cardiac function
PMID: 40496861
4
Decreased NDUFA2 expression in brain cortex associates with reduced Alzheimer's disease risk
PMID: 35902387
5
NDUFA2 shows prognostic significance in cervical squamous cell carcinoma
PMID: 40591190
6
NDUFA2 shows differential regulation in ovarian cancer drug resistance
PMID: 40036166
Disease Associationsβ“˜21
mitochondrial complex I deficiencyOpen Targets
0.67Moderate
mitochondrial complex I deficiency, nuclear type 13Open Targets
0.66Moderate
type 2 diabetes mellitusOpen Targets
0.61Moderate
diabetes mellitusOpen Targets
0.60Moderate
mitochondrial diseaseOpen Targets
0.60Moderate
Leigh syndromeOpen Targets
0.57Moderate
neurodegenerative diseaseOpen Targets
0.50Moderate
polycystic ovary syndromeOpen Targets
0.41Moderate
gestational diabetesOpen Targets
0.41Moderate
Insulin resistanceOpen Targets
0.40Moderate
obesityOpen Targets
0.40Weak
prediabetes syndromeOpen Targets
0.40Weak
metabolic syndromeOpen Targets
0.39Weak
type 1 diabetes mellitusOpen Targets
0.39Weak
Disorder of lipid metabolismOpen Targets
0.38Weak
agingOpen Targets
0.37Weak
cystic leukoencephalopathy without megalencephalyOpen Targets
0.37Weak
prostate cancerOpen Targets
0.36Weak
COVID-19Open Targets
0.36Weak
abnormal glucose toleranceOpen Targets
0.36Weak
Mitochondrial complex I deficiency, nuclear type 13UniProt
Pathogenic Variants3
NM_002488.5(NDUFA2):c.134A>C (p.Lys45Thr)Pathogenic
Cystic Leukoencephalopathy|Mitochondrial complex I deficiency, nuclear type 13
β˜…β˜†β˜†β˜†β†’ Residue 45
NM_002488.5(NDUFA2):c.170A>C (p.Glu57Ala)Pathogenic
Mitochondrial complex I deficiency, nuclear type 13
β˜†β˜†β˜†β˜†2020β†’ Residue 57
NM_002488.5(NDUFA2):c.208+5G>APathogenic
Mitochondrial complex I deficiency, nuclear type 13
β˜†β˜†β˜†β˜†2008
View on ClinVar β†—
Drug Targets3
ME-344Phase I/II
Mitochondrial complex I (NADH dehydrogenase) inhibitor
breast cancer
METFORMINApproved
Mitochondrial complex I (NADH dehydrogenase) inhibitor
diabetes mellitus
METFORMIN HYDROCHLORIDEApproved
Mitochondrial complex I (NADH dehydrogenase) inhibitor
type 2 diabetes mellitus
Related Genes
NDUFB5Protein interaction100%NDUFC1Protein interaction100%NDUFB8Protein interaction100%NDUFS6Protein interaction100%NDUFB2Protein interaction100%NDUFB7Protein interaction100%
Tissue Expression6 tissues
Liver
100%
Heart
86%
Bone Marrow
52%
Brain
50%
Lung
49%
Ovary
44%
Gene Interaction Network
Click a node to explore
NDUFA2NDUFB5NDUFC1NDUFB8NDUFS6NDUFB2NDUFB7
PROTEIN STRUCTURE
Preparing viewer…
PDB5XTB Β· 3.40 Γ… Β· EM
View on RCSB β†—
Constraintβ“˜
LOEUFβ“˜
1.34LoF Tolerant
pLIβ“˜
0.00Tolerant
Observed/Expected LoF0.77 [0.46–1.34]
RankingsWhere NDUFA2 stands among ~20K protein-coding genes
  • #6,921of 20,598
    Most Researched68
  • #631of 1,025
    FDA-Approved Drug Targets2
  • #4,035of 5,498
    Most Pathogenic Variants3
  • #14,059of 17,882
    Most Constrained (LOEUF)1.34
Genes detectedNDUFA2
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
Recessive mutations in NDUFA2 cause mitochondrial leukoencephalopathy.
PMID: 28857146
Clin Genet Β· 2018
1.00
2
PhosSNPs-Regulated Gene Network and Pathway Significant for Rheumatoid Arthritis.
PMID: 34569543
Hum Hered Β· 2021
0.90
3
NOC2L Promotes Paclitaxel Resistance in Various Types of Ovarian Cancers by Decreasing NDUFA4 through Histone Acetylation Suppression.
PMID: 40036166
Mol Cancer Ther Β· 2025
0.80
4
Ubiquitin proteasome system in Parkinson's disease: a keeper or a witness?
PMID: 22921536
Exp Neurol Β· 2012
0.70
5
Exploring the role of mitochondrial metabolism and immune infiltration in myocardial infarction: novel insights from bioinformatics and experimental validation.
PMID: 40496861
Front Immunol Β· 2025
0.60