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GeneE
50 sources retrieved Β· Most recent: April 2026 Β· Index updated 14 days ago
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RB1
RB transcriptional corepressor 1
Chromosome 13 Β· 13q14.2
NCBI Gene: 5925Ensembl: ENSG00000139687.17HGNC: HGNC:9884UniProt: A0A2R8YFL6
1,423PubMed Papers
23Diseases
0Drugs
944Pathogenic Variants
FUNCTIONAL ROLE
Highly ConstrainedHub GeneTranscription FactorTumor Suppressor
RESEARCH IMPACT
Highly StudiedTrendingVariant-Rich
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
negative regulation of gene expressionsister chromatid biorientationRb-E2F complexheterochromatin formationretinoblastomahereditary retinoblastomaurinary bladder cancerretinoblastoma (nonhereditary)
✦AI Summary

RB1 (RB transcriptional corepressor 1) is a tumor suppressor gene located on chromosome 13 that functions as a negative regulator of cell cycle progression and transcription. The protein acts as a transcriptional repressor by binding E2F1 and other transcription factors, thereby controlling the G1/S cell cycle checkpoint 1. RB1 regulates chromosome 13, heterochromatin formation, and mitotic progression through interactions with cyclin/CDK complexes and kinase binding [NCBI/GO annotations]. During viral infections, oncogenic proteins from SV40, HPV, and adenovirus disrupt the RB1-E2F1 complex, inactivating RB1's tumor suppressive function [UniProt]. RB1 mutations cause retinoblastoma, a pediatric eye malignancy requiring biallelic inactivation within retinal precursor cells 2. Germline RB1 mutations occur in 41.9% of retinoblastoma patients, with both small genetic rearrangements (78.9%) and large genomic rearrangements (21.1%) documented 3. Beyond retinoblastoma, concurrent RB1 and TP53 alterations identify high-risk EGFR-mutant lung cancers with 18% transformation to small cell carcinoma and significantly shortened survival (9.5 months vs. 36.6 months without dual mutations) 4. RB1 knockout in breast organoid models, combined with P53 and PTEN mutations, generates estrogen-receptor positive tumors responsive to endocrine therapy, supporting its role in multiple cancer subtypes 5. Genetic testing and counseling are essential for retinoblastoma patients to assess long-term malignancy risk and guide surveillance strategies.

Sources cited
1
RB1 is the first described human tumor suppressor gene playing an integral role in retinoblastoma development and serves as a negative regulator of transcription
PMID: 31683923
2
Mutations in both RB1 alleles within retinal precursor cells are essential for retinoblastoma development; germline status differentiation is crucial for prognosis assessment
PMID: 27488068
3
Germline RB1 mutations occur in 41.9% of retinoblastoma patients, with 78.9% small genetic rearrangements and 21.1% large genomic rearrangements
PMID: 37682130
4
Concurrent RB1 and TP53 alterations in EGFR-mutant lung cancers identify a subset at 18% risk for small cell transformation with shortened survival of 9.5 months
PMID: 31228622
5
RB1 knockout combined with P53 and PTEN mutations in breast organoids generates estrogen-receptor positive tumors responsive to endocrine therapy
PMID: 31589320
Disease Associationsβ“˜23
retinoblastomaOpen Targets
0.84Strong
hereditary retinoblastomaOpen Targets
0.81Strong
urinary bladder cancerOpen Targets
0.74Strong
retinoblastoma (nonhereditary)Open Targets
0.74Strong
urinary bladder carcinomaOpen Targets
0.74Strong
small cell lung carcinomaOpen Targets
0.72Strong
hepatocellular carcinomaOpen Targets
0.62Moderate
lung adenocarcinomaOpen Targets
0.61Moderate
osteosarcomaOpen Targets
0.59Moderate
cancerOpen Targets
0.58Moderate
hereditary neoplastic syndromeOpen Targets
0.57Moderate
Inherited cancer-predisposing syndromeOpen Targets
0.57Moderate
bone osteosarcomaOpen Targets
0.57Moderate
neurodegenerative diseaseOpen Targets
0.55Moderate
hypotrichosis 8Open Targets
0.55Moderate
breast adenocarcinomaOpen Targets
0.54Moderate
leiomyosarcomaOpen Targets
0.52Moderate
glioblastoma multiformeOpen Targets
0.52Moderate
non-small cell lung carcinomaOpen Targets
0.50Moderate
trilateral retinoblastomaOpen Targets
0.45Moderate
Bladder cancerUniProt
Childhood cancer retinoblastomaUniProt
Osteogenic sarcomaUniProt
Pathogenic Variants944
NM_000321.3(RB1):c.1399C>T (p.Arg467Ter)Pathogenic
not provided|Retinoblastoma|Hereditary cancer-predisposing syndrome
β˜…β˜…β˜†β˜†2026β†’ Residue 467
NM_000321.3(RB1):c.2094del (p.Arg698fs)Pathogenic
Retinoblastoma
β˜…β˜…β˜†β˜†2026β†’ Residue 698
NM_000321.3(RB1):c.1654C>T (p.Arg552Ter)Pathogenic
Retinoblastoma|Hereditary cancer-predisposing syndrome|Malignant tumor of urinary bladder|not provided
β˜…β˜…β˜†β˜†2026β†’ Residue 552
NM_000321.3(RB1):c.1981C>T (p.Arg661Trp)Pathogenic
Retinoblastoma|Hereditary cancer-predisposing syndrome|Small cell lung carcinoma;Bone osteosarcoma;Retinoblastoma;Malignant tumor of urinary bladder|not provided|Vulvar adenocarcinoma of mammary gland type|Hereditary retinoblastoma|Neoplasm
β˜…β˜…β˜†β˜†2026β†’ Residue 661
NM_000321.3(RB1):c.1049+1G>TPathogenic
Retinoblastoma|Hereditary cancer-predisposing syndrome
β˜…β˜…β˜†β˜†2026
NM_000321.3(RB1):c.772_776del (p.Asn258fs)Pathogenic
Retinoblastoma|Hereditary cancer-predisposing syndrome|not provided
β˜…β˜…β˜†β˜†2026β†’ Residue 258
NM_000321.3(RB1):c.1909C>T (p.Gln637Ter)Pathogenic
Retinoblastoma|Neoplasm|Hereditary cancer-predisposing syndrome
β˜…β˜…β˜†β˜†2026β†’ Residue 637
NM_000321.3(RB1):c.1389+5G>APathogenic
Hereditary cancer-predisposing syndrome|Retinoblastoma
β˜…β˜…β˜†β˜†2026
NM_000321.3(RB1):c.763C>T (p.Arg255Ter)Pathogenic
Retinoblastoma|Hereditary cancer-predisposing syndrome|not provided|Small cell lung carcinoma;Bone osteosarcoma;Retinoblastoma;Malignant tumor of urinary bladder|Neoplasm|Hereditary retinoblastoma
β˜…β˜…β˜†β˜†2026β†’ Residue 255
NM_000321.3(RB1):c.1306C>T (p.Gln436Ter)Pathogenic
Retinoblastoma
β˜…β˜…β˜†β˜†2026β†’ Residue 436
NM_000321.3(RB1):c.2663+1G>APathogenic
Retinoblastoma|Sarcoma
β˜…β˜…β˜†β˜†2026
NM_000321.3(RB1):c.1338C>A (p.Tyr446Ter)Pathogenic
Hereditary cancer-predisposing syndrome|Retinoblastoma|not provided
β˜…β˜…β˜†β˜†2026β†’ Residue 446
NM_000321.3(RB1):c.1814+1G>APathogenic
Hereditary cancer-predisposing syndrome|Malignant tumor of urinary bladder|Retinoblastoma
β˜…β˜…β˜†β˜†2026
NM_000321.3(RB1):c.967G>T (p.Glu323Ter)Pathogenic
Retinoblastoma
β˜…β˜…β˜†β˜†2026β†’ Residue 323
NM_000321.3(RB1):c.958C>T (p.Arg320Ter)Pathogenic
Retinoblastoma|Hereditary cancer-predisposing syndrome|not provided|Hereditary retinoblastoma
β˜…β˜…β˜†β˜†2025β†’ Residue 320
NM_000321.3(RB1):c.2117G>A (p.Cys706Tyr)Pathogenic
Retinoblastoma
β˜…β˜…β˜†β˜†2025β†’ Residue 706
NM_000321.3(RB1):c.751C>T (p.Arg251Ter)Pathogenic
Hereditary cancer-predisposing syndrome|Retinoblastoma|Neoplasm|not provided|Hereditary retinoblastoma
β˜…β˜…β˜†β˜†2025β†’ Residue 251
NM_000321.3(RB1):c.1333C>T (p.Arg445Ter)Pathogenic
Retinoblastoma|Hereditary cancer-predisposing syndrome|Small cell lung carcinoma;Bone osteosarcoma;Malignant tumor of urinary bladder;Retinoblastoma|not provided|Hereditary retinoblastoma
β˜…β˜…β˜†β˜†2025β†’ Residue 445
NM_000321.3(RB1):c.184C>T (p.Gln62Ter)Pathogenic
Retinoblastoma|Hereditary cancer-predisposing syndrome
β˜…β˜…β˜†β˜†2025β†’ Residue 62
NM_000321.3(RB1):c.45_79del (p.Ala16fs)Pathogenic
Retinoblastoma|not provided|Hereditary cancer-predisposing syndrome
β˜…β˜…β˜†β˜†2025β†’ Residue 16
View on ClinVar β†—
Related Genes
CCND1Protein interaction100%CCND2Protein interaction100%CCND3Protein interaction100%CCNE1Protein interaction100%CDK1Protein interaction100%CDK2Protein interaction100%
Tissue Expression6 tissues
Heart
100%
Bone Marrow
65%
Lung
64%
Brain
53%
Ovary
36%
Liver
29%
Gene Interaction Network
Click a node to explore
RB1CCND1CCND2CCND3CCNE1CDK1CDK2
PROTEIN STRUCTURE
Preparing viewer…
PDB2R7G Β· 1.67 Γ… Β· X-ray
View on RCSB β†—
Constraintβ“˜
LOEUFβ“˜
0.24Highly Constrained
pLIβ“˜
1.00Intolerant
Observed/Expected LoF0.16 [0.11–0.24]
RankingsWhere RB1 stands among ~20K protein-coding genes
  • #91of 20,598
    Most Researched1,423 Β· top 1%
  • #41of 5,498
    Most Pathogenic Variants944 Β· top 1%
  • #690of 17,882
    Most Constrained (LOEUF)0.24 Β· top 5%
Genes detectedRB1
Sources retrieved50 papers
Response timeβ€”
πŸ“„ Sources
50β–Ό
1
Ginsenoside Rb1 inhibits astrocyte activation and promotes transfer of astrocytic mitochondria to neurons against ischemic stroke.
PMID: 35696763
Redox Biol Β· 2022
1.00
2
Concurrent RB1 and TP53 Alterations Define aΒ Subset of EGFR-Mutant Lung Cancers at risk forΒ Histologic Transformation and Inferior Clinical Outcomes.
PMID: 31228622
J Thorac Oncol Β· 2019
0.90
3
Novel insights into RB1 mutation.
PMID: 35964818
Cancer Lett Β· 2022
0.84
4
RB1, p16, and Human Papillomavirus in Oropharyngeal Squamous Cell Carcinoma.
PMID: 33830464
Head Neck Pathol Β· 2021
0.80
5
Modeling Breast Cancer Using CRISPR-Cas9-Mediated Engineering of Human Breast Organoids.
PMID: 31589320
J Natl Cancer Inst Β· 2020
0.80