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10 sources retrieved · Most recent: April 2026 · Index updated 15 days ago
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SHOX2
SHOX homeobox 2
Chromosome 3 · 3q25.32
NCBI Gene: 6474Ensembl: ENSG00000168779.21HGNC: HGNC:10854UniProt: O60902
61PubMed Papers
20Diseases
0Drugs
0Pathogenic Variants
DATA QUALITY
✓ Experimental GO Evidence✓ Swiss-Prot Reviewed
regulation of heart rateDNA-binding transcription factor activity, RNA polymerase II-specificsequence-specific double-stranded DNA bindingnegative regulation of transcription by RNA polymerase IIalcohol drinkingmajor depressive disordersmoking initiationsubstance-related disorder
✦AI Summary

SHOX2 encodes a transcription factor essential for cardiac pacemaker development and skeletal morphogenesis 1. The gene contains a complex cis-regulatory architecture with a gene desert flanking its locus that orchestrates pleiotropic developmental expression through tissue-specific enhancers, controlling proximal limb, craniofacial, and cardiac sinus venosus development 1. SHOX2 is crucial for sinoatrial node differentiation and cardiac conduction system formation 2. Loss-of-function mutations impair pacemaker function; notably, a 3'UTR variant (c.*28T>C) associates with early-onset atrial fibrillation by creating a binding site for miR-92b-5p, resulting in reduced SHOX2 expression in atrial tissue 3. Clinically, SHOX2 has significant diagnostic utility in cancer detection. SHOX2 promoter methylation demonstrates 85% sensitivity and 92% specificity for malignant pleural effusion detection 4, and 77% sensitivity and 90% specificity for lung cancer diagnosis when combined with RASSF1A methylation 5. These epigenetic biomarkers outperform conventional cytological methods for early-stage lung cancer screening 6. The gene functions as both a developmental regulator controlling organ morphogenesis and a cancer-associated biomarker whose aberrant methylation indicates malignant transformation.

Sources cited
1
SHOX2 encodes a transcription factor indispensable for proximal limb, craniofacial, and cardiac pacemaker development; gene desert contains multiple tissue-specific enhancers controlling pleiotropic expression
PMID: 39389973
2
SHOX2 is crucial for sinoatrial node differentiation and cardiac conduction system formation; mutations cause bradycardiac arrhythmias
PMID: 29503396
3
SHOX2 missense mutations affect pacemaker function; 3'UTR variant associates with early-onset atrial fibrillation via miR-92b-5p binding
PMID: 27138930
4
SHOX2 and RASSF1A methylation show 85% sensitivity and 92% specificity for detecting malignant pleural effusion
PMID: 40614167
5
RASSF1A and SHOX2 DNA methylation combined show 77% sensitivity, 90% specificity, and 0.92 AUC for lung cancer diagnosis
PMID: 39686414
6
SHOX2 methylation detection has higher sensitivity and specificity than common diagnostic methods for lung cancer, especially early stage
PMID: 32266538
7
SHOX2 promoter methylation shows 63% sensitivity, 91% specificity, and 0.88 AUC for lung cancer diagnosis
PMID: 34741433
8
SHOX2 promoter hypermethylation demonstrates 75% sensitivity and 89% specificity for lung cancer diagnosis; present in serum, bronchoalveolar fluid, and pleural effusion
PMID: 34275516
Disease Associationsⓘ20
alcohol drinkingOpen Targets
0.27Weak
major depressive disorderOpen Targets
0.24Weak
smoking initiationOpen Targets
0.23Weak
substance-related disorderOpen Targets
0.21Weak
attention deficit hyperactivity disorderOpen Targets
0.20Weak
peripheral vascular diseaseOpen Targets
0.19Weak
depressive disorderOpen Targets
0.17Weak
autism spectrum disorderOpen Targets
0.16Weak
lobe attachmentOpen Targets
0.16Weak
bipolar disorderOpen Targets
0.16Weak
anorexia nervosaOpen Targets
0.15Weak
obsessive-compulsive disorderOpen Targets
0.15Weak
schizophreniaOpen Targets
0.14Weak
ovarian neoplasmOpen Targets
0.14Weak
Tourette syndromeOpen Targets
0.13Weak
osteomyelitisOpen Targets
0.13Weak
substance abuseOpen Targets
0.13Weak
mood disorderOpen Targets
0.12Weak
handednessOpen Targets
0.12Weak
atrial fibrillationOpen Targets
0.11Weak
Pathogenic Variants
No pathogenic variants reported on ClinVar for this gene.
View on ClinVar ↗
Related Genes
TBX18Protein interaction74%TBX3Protein interaction74%HCN4Protein interaction72%DLX6Shared pathway25%GDF11Shared pathway18%CNTNAP3BShared pathway17%
Tissue Expression6 tissues
Brain
100%
Heart
26%
Lung
7%
Ovary
5%
Bone Marrow
1%
Liver
1%
Gene Interaction Network
Click a node to explore
SHOX2TBX18TBX3HCN4DLX6GDF11CNTNAP3B
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted · UniProt O60902
View on AlphaFold ↗
Constraintⓘ
LOEUFⓘ
0.77LoF Tolerant
pLIⓘ
0.08Tolerant
Observed/Expected LoF0.46 [0.29–0.77]
RankingsWhere SHOX2 stands among ~20K protein-coding genes
  • #7,608of 20,598
    Most Researched61
  • #6,228of 17,882
    Most Constrained (LOEUF)0.77
Genes detectedSHOX2
Sources retrieved10 papers
Response time—
📄 Sources
10▼
1
A gene desert required for regulatory control of pleiotropic Shox2 expression and embryonic survival.
PMID: 39389973
Nat Commun · 2024
1.00
2
Diagnostic performance of SHOX2 and RASSF1A gene methylation assays in malignant pleural effusion: A systematic review and meta-analysis.
PMID: 40614167
Cancer Cytopathol · 2025
0.90
3
Signaling pathways and clinical application of RASSF1A and SHOX2 in lung cancer.
PMID: 32266538
J Cancer Res Clin Oncol · 2020
0.80
4
Shox2: The Role in Differentiation and Development of Cardiac Conduction System.
PMID: 29503396
Tohoku J Exp Med · 2018
0.70
5
Coding and non-coding variants in the SHOX2 gene in patients with early-onset atrial fibrillation.
PMID: 27138930
Basic Res Cardiol · 2016
0.60