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GeneE
27 sources retrieved Β· Most recent: April 2026 Β· Index updated 14 days ago
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TBX5
T-box transcription factor 5
Chromosome 12 Β· 12q24.21
NCBI Gene: 6910Ensembl: ENSG00000089225.21HGNC: HGNC:11604UniProt: Q99593
160PubMed Papers
21Diseases
0Drugs
195Pathogenic Variants
FUNCTIONAL ROLE
Highly ConstrainedTranscription Factor
RESEARCH IMPACT
TrendingVariant-Rich
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
DNA bindingcytoplasmnegative regulation of cell population proliferationnucleusHolt-Oram syndromeatrial fibrillationaortic valve disease 2Abnormality of the cardiovascular system
✦AI Summary

TBX5 is a T-box transcription factor essential for cardiac and forelimb development, functioning primarily as a transcriptional activator 1. During early cardiogenesis, TBX5 activates genes associated with cardiomyocyte maturation and septation signaling, while later in development it patterns the cardiac conduction system and maintains mature cardiomyocyte function 1. TBX5 maintains atrial identity by binding to an atrial-specific enhancer network and regulating chr12 architecture in post-natal cardiomyocytes 2. The protein interacts with other cardiac transcription factors in developmental networks 34, and cooperates with factors like MEF2C and PHF7 in fibroblast reprogramming toward cardiomyocytes 5. Dominant mutations in TBX5 cause Holt-Oram syndrome, characterized by congenital heart defects (septal defects, arrhythmias) and forelimb abnormalities 67. A systematic review identified 108 TBX5 variants in 277 patients, revealing a genotype-phenotype relationship: missense variants cluster in the T-box domain and associate with increased arrhythmia risk (48% vs 30%), while protein-truncating variants more frequently cause limb abnormalities (85% vs 64%) 6. These findings underscore TBX5's critical role in maintaining both cardiac structure and conduction system function.

Sources cited
1
TBX5 acts as transcriptional activator in cardiac development, with roles in cardiomyocyte maturation, septation, and cardiac conduction system patterning
PMID: 28057264
2
TBX5 maintains atrial identity by binding to atrial-specific enhancers and preserving tissue-specific chromatin architecture
PMID: 38344303
3
TBX5 protein interactomes in cardiac progenitors reveal genetic determinants of congenital heart disease
PMID: 35182466
4
TBX5 cooperates with MEF2C and PHF7 in fibroblast-to-cardiomyocyte reprogramming
PMID: 40631661
5
TBX5 is a core cardiac transcription factor that regulates other factors and acts combinatorially on downstream targets
PMID: 38884718
6
TBX5 variants cause Holt-Oram syndrome with genotype-phenotype relationship: missense variants associate with arrhythmias; truncating variants with limb defects
PMID: 38336121
7
TBX5 mutations cause Holt-Oram syndrome with cardiac and forelimb defects, with molecular basis reviewed for missense, extended protein, and duplication mutations
PMID: 25680289
Disease Associationsβ“˜21
Holt-Oram syndromeOpen Targets
0.83Strong
atrial fibrillationOpen Targets
0.56Moderate
aortic valve disease 2Open Targets
0.56Moderate
Abnormality of the cardiovascular systemOpen Targets
0.53Moderate
Abnormality of the skeletal systemOpen Targets
0.52Moderate
atrial flutterOpen Targets
0.48Moderate
congenital heart diseaseOpen Targets
0.47Moderate
cardiac arrhythmiaOpen Targets
0.47Moderate
neurodegenerative diseaseOpen Targets
0.46Moderate
hypertensionOpen Targets
0.44Moderate
heart diseaseOpen Targets
0.44Moderate
coronary atherosclerosisOpen Targets
0.41Moderate
osteoarthritis, kneeOpen Targets
0.41Moderate
Brugada syndromeOpen Targets
0.41Moderate
Abnormal heart morphologyOpen Targets
0.40Weak
atrioventricular blockOpen Targets
0.39Weak
Romano-Ward syndromeOpen Targets
0.39Weak
First degree atrioventricular blockOpen Targets
0.37Weak
polydactylyOpen Targets
0.37Weak
atrial septal defect, ostium secundum typeOpen Targets
0.35Weak
Holt-Oram syndromeUniProt
Pathogenic Variants195
NM_181486.4(TBX5):c.261C>G (p.Tyr87Ter)Pathogenic
Holt-Oram syndrome|Cardiovascular phenotype
β˜…β˜…β˜†β˜†2025β†’ Residue 87
NM_181486.4(TBX5):c.456del (p.Val153fs)Pathogenic
Aortic valve disease 2|not provided
β˜…β˜…β˜†β˜†2025β†’ Residue 153
NM_181486.4(TBX5):c.710G>A (p.Arg237Gln)Pathogenic
Holt-Oram syndrome|not provided|Aortic valve disease 2|Cardiovascular phenotype
β˜…β˜…β˜†β˜†2025β†’ Residue 237
NM_181486.4(TBX5):c.148-2A>GPathogenic
Holt-Oram syndrome|not provided|Aortic valve disease 2
β˜…β˜…β˜†β˜†2025
NM_181486.4(TBX5):c.242+1G>APathogenic
not provided|Holt-Oram syndrome
β˜…β˜…β˜†β˜†2025
NM_181486.4(TBX5):c.668C>T (p.Thr223Met)Pathogenic
not provided|Aortic valve disease 2|Holt-Oram syndrome
β˜…β˜…β˜†β˜†2025β†’ Residue 223
NM_181486.4(TBX5):c.105del (p.Ser36fs)Pathogenic
Holt-Oram syndrome|Aortic valve disease 2
β˜…β˜…β˜†β˜†2025β†’ Residue 36
NM_181486.4(TBX5):c.755G>C (p.Ser252Thr)Likely pathogenic
not provided|Holt-Oram syndrome|Aortic valve disease 2
β˜…β˜…β˜†β˜†2025β†’ Residue 252
NM_181486.4(TBX5):c.755G>T (p.Ser252Ile)Pathogenic
Aortic valve disease 2|not provided
β˜…β˜…β˜†β˜†2025β†’ Residue 252
NM_181486.4(TBX5):c.1485del (p.Thr496fs)Likely pathogenic
Cardiovascular phenotype|Aortic valve disease 2
β˜…β˜…β˜†β˜†2025β†’ Residue 496
NM_181486.4(TBX5):c.408C>G (p.Tyr136Ter)Pathogenic
not provided|Holt-Oram syndrome
β˜…β˜…β˜†β˜†2025β†’ Residue 136
NM_181486.4(TBX5):c.873C>A (p.Tyr291Ter)Pathogenic
not provided|Holt-Oram syndrome
β˜…β˜…β˜†β˜†2024β†’ Residue 291
NM_181486.4(TBX5):c.982+2T>GPathogenic
Aortic valve disease 2|Cardiovascular phenotype
β˜…β˜…β˜†β˜†2024
NM_181486.4(TBX5):c.835C>T (p.Arg279Ter)Pathogenic
not provided|Aortic valve disease 2|Holt-Oram syndrome|TBX5-related disorder
β˜…β˜…β˜†β˜†2024β†’ Residue 279
NM_181486.4(TBX5):c.587C>A (p.Ser196Ter)Pathogenic
not provided|Aortic valve disease 2|Holt-Oram syndrome|Cardiovascular phenotype
β˜…β˜…β˜†β˜†2024β†’ Residue 196
NM_181486.4(TBX5):c.1126C>T (p.Gln376Ter)Likely pathogenic
not provided|Holt-Oram syndrome
β˜…β˜…β˜†β˜†2023β†’ Residue 376
NM_181486.4(TBX5):c.593dup (p.Asn198fs)Pathogenic
Holt-Oram syndrome|Aortic valve disease 2
β˜…β˜…β˜†β˜†2023β†’ Residue 198
NM_181486.4(TBX5):c.408C>A (p.Tyr136Ter)Pathogenic
Holt-Oram syndrome|TBX5-related disorder
β˜…β˜…β˜†β˜†2023β†’ Residue 136
NM_181486.4(TBX5):c.205G>T (p.Glu69Ter)Pathogenic
Holt-Oram syndrome|not provided
β˜…β˜…β˜†β˜†2023β†’ Residue 69
NM_181486.4(TBX5):c.611dup (p.His204fs)Pathogenic
not provided|Aortic valve disease 2
β˜…β˜…β˜†β˜†2022β†’ Residue 204
View on ClinVar β†—
Related Genes
SMARCA4Protein interaction100%YAP1Protein interaction99%SMARCD3Protein interaction96%MYH6Protein interaction91%NPPAProtein interaction91%BANF1Protein interaction88%
Tissue Expression6 tissues
Heart
100%
Lung
43%
Brain
0%
Liver
0%
Ovary
0%
Bone Marrow
0%
Gene Interaction Network
Click a node to explore
TBX5SMARCA4YAP1SMARCD3MYH6NPPABANF1
PROTEIN STRUCTURE
Preparing viewer…
PDB2X6U Β· 1.90 Γ… Β· X-ray
View on RCSB β†—
Constraintβ“˜
LOEUFβ“˜
0.27Highly Constrained
pLIβ“˜
1.00Intolerant
Observed/Expected LoF0.15 [0.09–0.27]
RankingsWhere TBX5 stands among ~20K protein-coding genes
  • #2,816of 20,598
    Most Researched160 Β· top quartile
  • #356of 5,498
    Most Pathogenic Variants195 Β· top 10%
  • #888of 17,882
    Most Constrained (LOEUF)0.27 Β· top 5%
Genes detectedTBX5
Sources retrieved27 papers
Response timeβ€”
πŸ“„ Sources
27β–Ό
1
Transcription factor protein interactomes reveal genetic determinants in heart disease.
PMID: 35182466
Cell Β· 2022
1.00
2
TBX5 variants and cardiac phenotype: A systematic review of the literature and a novel variant.
PMID: 38336121
Eur J Med Genet Β· 2024
0.90
3
The human TBX5 gene mutation database.
PMID: 16134140
Hum Mutat Β· 2005
0.84
4
Cellular Reprogramming by PHF7 Enhances Cardiac Function Following Myocardial Infarction.
PMID: 40631661
Circulation Β· 2025
0.80
5
Molecular basis of the clinical features of Holt-Oram syndrome resulting from missense and extended protein mutations of the TBX5 gene as well as TBX5 intragenic duplications.
PMID: 25680289
Gene Β· 2015
0.70