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GeneE
10 sources retrieved Β· Most recent: April 2026 Β· Index updated 15 days ago
β“˜GeneE is for informational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment.
TMEM107
transmembrane protein 107
Chromosome 17 Β· 17p13.1
NCBI Gene: 84314Ensembl: ENSG00000179029.15HGNC: HGNC:28128UniProt: E9PIH0
23PubMed Papers
22Diseases
0Drugs
9Pathogenic Variants
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
protein bindingcilium assemblynon-motile cilium assemblyciliary transition zoneMeckel syndrome 13orofaciodigital syndrome 16orofaciodigital syndromeleukoencephalopathy with calcifications and cysts
✦AI Summary

TMEM107 is a transmembrane protein localized to the ciliary transition zone that plays a critical role in ciliogenesis and primary cilia protein composition 1. During cilia formation, TMEM107 regulates the localization of MKS complex proteins to the ciliary transition zone and controls overall ciliary protein content 1. TMEM107 functions as a negative regulator of Hedgehog (Hh) signaling; loss of TMEM107 expression leads to ectopic activation of the SHH pathway and upregulation of GLI1 target genes 23. TMEM107 is essential for proper eye development, as Tmem107-deficient mice exhibit anophthalmia and microphthalmia with impaired retinal differentiation 2. TMEM107 deficiency in retinal organoids results in loss of primary cilia and cyst formation 2. Biallelic TMEM107 mutations cause Meckel-Gruber syndrome (MKS13) and Orofaciodigital syndrome (OFD16), both ciliopathies characterized by developmental abnormalities 41. Patients and animal models with TMEM107 mutations display marked ciliogenesis defects, abnormal cilia length, polydactyly, and reduced ciliated cell numbers 14. Additionally, TMEM107 variants are associated with congenital heart defects, particularly heterotaxy, through its role in ciliogenesis 5. Loss of TMEM107 in cancer cells promotes epithelial-mesenchymal transition and invasion through Hh pathway activation, suggesting tumor-suppressive functions 3.

Sources cited
1
TMEM107 regulates ciliary transition zone protein localization and overall ciliary protein composition; mutations cause orofaciodigital syndrome
PMID: 26518474
2
TMEM107 is essential for eye development and ciliogenesis; deficiency causes anophthalmia, microphthalmia, and impaired retinal differentiation; TMEM107 loss prevents primary cilia formation and impairs Hh signaling response
PMID: 37863656
3
TMEM107 negatively regulates Hedgehog signaling and inhibits EMT and invasion in NSCLC cells; downregulation activates GLI1 and promotes metastatic phenotypes
PMID: 33124203
4
TMEM107 mutations cause Meckel-Gruber syndrome type 13; patient fibroblasts show ciliogenesis defects and Shh signaling perturbation
PMID: 26123494
5
TMEM107 variants are significantly associated with congenital heart defects, particularly heterotaxy, through its role in ciliogenesis
PMID: 37341229
6
TMEM107 expression is reduced in cells with minor intron splicing defects, contributing to primary cilia abnormalities and disrupted Hh signaling in orofaciodigital syndrome
PMID: 36084634
7
TMEM107 is a differentially spliced target in minor spliceosome defects; TMEM107 dysregulation contributes to abnormal cilia formation in OFD-related ciliopathies
PMID: 38158857
8
TMEM107 expression is diminished in minor spliceosome defects, leading to defective cilia and association with OFD and ciliary abnormalities
PMID: 41291844
Disease Associationsβ“˜22
Meckel syndrome 13Open Targets
0.68Moderate
orofaciodigital syndrome 16Open Targets
0.68Moderate
orofaciodigital syndromeOpen Targets
0.66Moderate
Coats plus syndromeOpen Targets
0.56Moderate
leukoencephalopathy with calcifications and cystsOpen Targets
0.56Moderate
Meckel syndromeOpen Targets
0.53Moderate
Joubert syndrome 29Open Targets
0.45Moderate
orofaciodigital syndrome IOpen Targets
0.19Weak
genetic disorderOpen Targets
0.19Weak
Meckel syndrome, type 1Open Targets
0.12Weak
non-small cell lung carcinomaOpen Targets
0.08Suggestive
polydactyly of a triphalangeal thumbOpen Targets
0.07Suggestive
Syndactyly type 2Open Targets
0.07Suggestive
syndactyly type 4Open Targets
0.07Suggestive
Triphalangeal thumb - polysyndactyly syndromeOpen Targets
0.06Suggestive
holoprosencephalyOpen Targets
0.06Suggestive
polydactyly of a biphalangeal thumbOpen Targets
0.06Suggestive
PolysyndactylyOpen Targets
0.06Suggestive
polysyndactyly 4Open Targets
0.06Suggestive
polydactyly of an index fingerOpen Targets
0.06Suggestive
Meckel syndrome 13UniProt
Orofaciodigital syndrome 16UniProt
Pathogenic Variants9
NM_183065.4(TMEM107):c.182dup (p.Leu63fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 63
NM_183065.4(TMEM107):c.218C>G (p.Ser73Ter)Pathogenic
Meckel syndrome 13
β˜…β˜†β˜†β˜†2024β†’ Residue 73
NM_183065.4(TMEM107):c.191_192del (p.Phe64fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2024β†’ Residue 64
NM_183065.4(TMEM107):c.256+1G>APathogenic
Meckel syndrome 13
β˜…β˜†β˜†β˜†2024
NM_183065.4(TMEM107):c.257-1delLikely pathogenic
not provided
β˜…β˜†β˜†β˜†2024
NM_183065.4(TMEM107):c.22del (p.Val8fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2024β†’ Residue 8
NM_183065.4(TMEM107):c.134A>G (p.Glu45Gly)Pathogenic
Orofaciodigital syndrome 16|not provided|Leukoencephalopathy with calcifications and cysts
β˜…β˜†β˜†β˜†2023β†’ Residue 45
NM_183065.4(TMEM107):c.295TTC[1] (p.Phe100del)Pathogenic
Orofaciodigital syndrome 16|Orofaciodigital syndrome|Joubert syndrome 29
β˜…β˜†β˜†β˜†2015β†’ Residue 100
NM_183065.4(TMEM107):c.384del (p.Leu128fs)Pathogenic
Meckel syndrome 13
β˜†β˜†β˜†β˜†2017β†’ Residue 128
View on ClinVar β†—
Related Genes
NPHP1Protein interaction94%TCTN3Protein interaction94%B9D1Protein interaction94%AHI1Protein interaction94%TMEM231Protein interaction94%NPHP4Protein interaction88%
Tissue Expression6 tissues
Bone Marrow
100%
Brain
88%
Heart
39%
Lung
38%
Ovary
37%
Liver
19%
Gene Interaction Network
Click a node to explore
TMEM107NPHP1TCTN3B9D1AHI1TMEM231NPHP4
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted Β· UniProt Q6UX40
View on AlphaFold β†—
Constraintβ“˜
LOEUFβ“˜
1.49LoF Tolerant
pLIβ“˜
0.00Tolerant
Observed/Expected LoF1.01 [0.70–1.49]
RankingsWhere TMEM107 stands among ~20K protein-coding genes
  • #13,544of 20,598
    Most Researched23
  • #2,996of 5,498
    Most Pathogenic Variants9
  • #15,137of 17,882
    Most Constrained (LOEUF)1.49
Genes detectedTMEM107
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
PMID: 20301500
1.00
2
Mutations in SCNM1 cause orofaciodigital syndrome due to minor intron splicing defects affecting primary cilia.
PMID: 36084634
Am J Hum Genet Β· 2022
0.90
3
Role of ciliopathy protein TMEM107 in eye development: insights from a mouse model and retinal organoid.
PMID: 37863656
Life Sci Alliance Β· 2023
0.80
4
A gene-based association test of interactions for maternal-fetal genotypes identifies genes associated with nonsyndromic congenital heart defects.
PMID: 37341229
Genet Epidemiol Β· 2023
0.70
5
TMEM107 Is a Critical Regulator of Ciliary Protein Composition and Is Mutated in Orofaciodigital Syndrome.
PMID: 26518474
Hum Mutat Β· 2016
0.60