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10 sources retrieved · Most recent: April 2026 · Index updated 15 days ago
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TSPYL1
TSPY like 1
Chromosome 6 · 6q22.1
NCBI Gene: 7259Ensembl: ENSG00000189241.8HGNC: HGNC:12382UniProt: Q9H0U9
73PubMed Papers
21Diseases
0Drugs
2Pathogenic Variants
CLINICAL
OMIM Disease Gene
DATA QUALITY
✓ Experimental GO Evidence✓ Swiss-Prot Reviewed
enzyme bindingnucleolusnucleoplasmnucleussudden infant death-dysgenesis of the testes syndromeSudden infant death - dysgenesis of the testesneurodegenerative diseasegenetic disorder
✦AI Summary

TSPYL1 is a nucleosome assembly protein (NAP) and histone chaperone that functions as a critical regulator of TGFβ signaling and cell cycle progression 1. The protein localizes to the nucleus and binds chr6 and histones, partnering with transcription factor FOXA1 and histone methyltransferase EZH2 to repress TGFBR1 expression and epithelial-mesenchymal transition 1. TSPYL1 depletion increases TGFβ signaling through elevated TGFBR1 expression and TSPYL2 protein stability, disrupting this counter-balancing regulatory axis 1. TSPYL1 deficiency causes autosomal recessive sudden infant death with dysgenesis of the testes syndrome (SIDDT), characterized by visceroautonomic dysfunction, progressive neurological abnormalities, testicular dysgenesis, and brainstem-mediated cardiorespiratory arrest 2. Pathogenic mutations result in mislocaliza of truncated protein to the Golgi, disrupting nuclear function and causing prolonged S and G2 cell cycle phases with reduced proliferation 2. TSPYL1 also regulates expression of cytochrome P450 genes including CYP3A4, with a common SNP (Pro62Ser) affecting abiraterone metabolism and prostate cancer drug response 3. While TSPYL1 mutations are associated with 46,XY disorders of sex development and male infertility cases, screening studies suggest limited diagnostic utility for idiopathic male infertility in general populations 4 5.

Sources cited
1
TSPYL1 is a nucleosome assembly protein and histone chaperone that represses TGFBR1 and regulates TGFβ signaling through partnership with FOXA1 and EZH2
PMID: 38588050
2
TSPYL1 deficiency causes lethal combined nervous and reproductive disease with visceroautonomic dysfunction, neurological abnormalities, testicular dysgenesis, and sudden infant death
PMID: 33075815
3
Pathogenic TSPYL1 mutations cause protein mislocalization to Golgi and disrupt cell cycle progression with prolonged S and G2 phases
PMID: 33075815
4
TSPYL1 regulates CYP3A4 expression and a common SNP (Pro62Ser) affects abiraterone metabolism and prostate cancer treatment response
PMID: 29027195
5
TSPYL1 mutations are associated with 46,XY disorder of sex development and male infertility cases
PMID: 19463995
6
TSPYL1 mutation screening does not show significant association with idiopathic male infertility and is not recommended for routine diagnostics
PMID: 22137496
Disease Associationsⓘ21
sudden infant death-dysgenesis of the testes syndromeOpen Targets
0.71Strong
Sudden infant death - dysgenesis of the testesOpen Targets
0.68Moderate
neurodegenerative diseaseOpen Targets
0.47Moderate
genetic disorderOpen Targets
0.19Weak
brain compressionOpen Targets
0.12Weak
edemaOpen Targets
0.12Weak
systemic lupus erythematosusOpen Targets
0.08Suggestive
depressive disorderOpen Targets
0.06Suggestive
Griscelli diseaseOpen Targets
0.05Suggestive
major depressive disorderOpen Targets
0.05Suggestive
uncombable hair syndromeOpen Targets
0.04Suggestive
Griscelli disease type 3Open Targets
0.04Suggestive
Griscelli syndrome type 3Open Targets
0.04Suggestive
Griscelli disease type 1Open Targets
0.04Suggestive
Griscelli syndrome type 1Open Targets
0.04Suggestive
Piebald trait - neurologic defectsOpen Targets
0.03Suggestive
piebald trait-neurologic defects syndromeOpen Targets
0.03Suggestive
hypotrichosis 8Open Targets
0.03Suggestive
isolated familial wooly hair disorderOpen Targets
0.03Suggestive
Woolly hairOpen Targets
0.03Suggestive
Sudden infant death with dysgenesis of the testes syndromeUniProt
Pathogenic Variants2
NM_003309.4(TSPYL1):c.725_726del (p.Val242fs)Pathogenic
Sudden infant death-dysgenesis of the testes syndrome
★★☆☆2024→ Residue 242
NM_003309.4(TSPYL1):c.460dup (p.Glu154fs)Pathogenic
Sudden infant death-dysgenesis of the testes syndrome
☆☆☆☆2004→ Residue 154
View on ClinVar ↗
Related Genes
TSPY10Shared pathway100%TSPY8Shared pathway100%TSPY4Shared pathway100%TSPY3Shared pathway100%TSPY9Shared pathway100%TSPYL6Shared pathway100%
Tissue Expression6 tissues
Brain
100%
Heart
41%
Bone Marrow
40%
Liver
23%
Ovary
20%
Lung
13%
Gene Interaction Network
Click a node to explore
TSPYL1TSPY10TSPY8TSPY4TSPY3TSPY9TSPYL6
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted · UniProt Q9H0U9
View on AlphaFold ↗
Constraintⓘ
LOEUFⓘ
1.06LoF Tolerant
pLIⓘ
0.00Tolerant
Observed/Expected LoF0.70 [0.47–1.06]
RankingsWhere TSPYL1 stands among ~20K protein-coding genes
  • #6,520of 20,598
    Most Researched73
  • #4,374of 5,498
    Most Pathogenic Variants2
  • #10,593of 17,882
    Most Constrained (LOEUF)1.06
Genes detectedTSPYL1
Sources retrieved10 papers
Response time—
📄 Sources
10▼
1
TSPYL1 as a Critical Regulator of TGFβ Signaling through Repression of TGFBR1 and TSPYL2.
PMID: 38588050
Adv Sci (Weinh) · 2024
1.00
2
Mutations in the TSPYL1 gene associated with 46,XY disorder of sex development and male infertility.
PMID: 19463995
Fertil Steril · 2009
0.90
3
Unravelling the disease mechanism for TSPYL1 deficiency.
PMID: 33075815
Hum Mol Genet · 2020
0.80
4
TSPYL Family Regulates CYP17A1 and CYP3A4 Expression: Potential Mechanism Contributing to Abiraterone Response in Metastatic Castration-Resistant Prostate Cancer.
PMID: 29027195
Clin Pharmacol Ther · 2018
0.70
5
Genetic investigation of the TSPYL1 gene in sudden infant death syndrome.
PMID: 16418600
Genet Med · 2006
0.60