HomeAboutRankingsData Sources
Β© 2026 GeneE
🧬
GeneE
11 sources retrieved Β· Most recent: April 2026 Β· Index updated 14 days ago
β“˜GeneE is for informational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment.
IARS1
isoleucyl-tRNA synthetase 1
Chromosome 9 Β· 9q22.31
NCBI Gene: 3376Ensembl: ENSG00000196305.19HGNC: HGNC:5330UniProt: A0A804HJN6
252PubMed Papers
21Diseases
0Drugs
37Pathogenic Variants
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
isoleucyl-tRNA aminoacylationprotein bindingGTPase bindingosteoblast differentiationgrowth retardation, intellectual developmental disorder, hypotonia, and hepatopathyGlobal developmental delaymicrocephalyAbnormality of the skeletal system
✦AI Summary

IARS1 (isoleucyl-tRNA synthetase 1) catalyzes the attachment of isoleucine to its cognate tRNA through a two-step ATP-dependent reaction, enabling accurate protein synthesis 1. The enzyme functions primarily in the cytoplasm and requires t6A modification on tRNAIle for optimal aminoacylation activity 2. IARS1 is essential for embryonic development, as complete knockout causes post-implantation embryonic lethality in mice before organogenesis completion 3. Mutations in IARS1 cause Growth Retardation, Impaired intellectual development, hypotonia, and Hepatopathy (GRIDHH), a rare mitochondrial disease with diverse clinical presentations 4. Key pathological features include intrauterine growth retardation, hepatic dysfunction with fibrosis and steatosis, microcephaly, neurodevelopmental delay, and hypotonia 4. At the molecular level, IARS1 mutations impair mitochondrial function by decreasing mitochondrial membrane potential, increasing reactive oxygen species, and reducing expression of mitochondrial proteins like NME4 5. Clinically, IARS1-deficient individuals present with failure to thrive, feeding difficulties, elevated liver enzymes, cholestasis, and recurrent infections 4. Notably, pulmonary alveolar proteinosis and anemia are associated with poor prognosis 4. Interestingly, under isoleucine deprivation, IARS1 can incorporate valine into proteins at isoleucine codons, a compensatory mechanism absent in IARS1-deficient cells 6.

Sources cited
1
IARS1 catalyzes attachment of amino acids to tRNA; mutations cause growth retardation and liver dysfunction
PMID: 39062673
2
t6A modification is required for IARS1-mediated tRNAIle aminoacylation and proper codon decoding
PMID: 35104889
3
IARS1 is essential for embryonic development; homozygous knockout mice are embryonic lethal
PMID: 41192854
4
IARS1 mutations cause GRIDHH with intrauterine growth retardation, hepatic dysfunction, microcephaly, and neurodevelopmental delay; pulmonary alveolar proteinosis and anemia predict poor prognosis
PMID: 40635052
5
IARS1 mutations impair mitochondrial function by decreasing membrane potential, increasing ROS, and reducing NME4 expression
PMID: 37108118
6
IARS1 can incorporate valine at isoleucine codons during isoleucine deprivation; this compensatory mechanism is absent in IARS1-deficient cells
PMID: 39657787
Disease Associationsβ“˜21
growth retardation, intellectual developmental disorder, hypotonia, and hepatopathyOpen Targets
0.73Strong
Global developmental delayOpen Targets
0.29Weak
microcephalyOpen Targets
0.29Weak
Abnormality of the skeletal systemOpen Targets
0.21Weak
genetic disorderOpen Targets
0.15Weak
Hallux valgusOpen Targets
0.14Weak
neoplasmOpen Targets
0.06Suggestive
non-small cell lung carcinomaOpen Targets
0.05Suggestive
glycogen storage disease VIOpen Targets
0.04Suggestive
transient infantile hypertriglyceridemia and hepatosteatosisOpen Targets
0.04Suggestive
non-alcoholic fatty liver diseaseOpen Targets
0.04Suggestive
atrial fibrillationOpen Targets
0.04Suggestive
Insulin resistanceOpen Targets
0.03Suggestive
breast cancerOpen Targets
0.03Suggestive
hepatocellular carcinomaOpen Targets
0.03Suggestive
gestational diabetesOpen Targets
0.03Suggestive
Alzheimer diseaseOpen Targets
0.03Suggestive
cancerOpen Targets
0.03Suggestive
retinoblastomaOpen Targets
0.03Suggestive
colorectal carcinomaOpen Targets
0.03Suggestive
Growth retardation, impaired intellectual development, hypotonia, and hepatopathyUniProt
Pathogenic Variants37
NM_002161.6(IARS1):c.3461_3462del (p.Val1154fs)Pathogenic
not provided|Growth retardation, intellectual developmental disorder, hypotonia, and hepatopathy
β˜…β˜…β˜†β˜†2026β†’ Residue 1154
NM_002161.6(IARS1):c.3377dup (p.Asn1126fs)Pathogenic
not provided|Growth retardation, intellectual developmental disorder, hypotonia, and hepatopathy
β˜…β˜…β˜†β˜†2025β†’ Residue 1126
NM_002161.6(IARS1):c.213T>G (p.Tyr71Ter)Pathogenic
Growth retardation, intellectual developmental disorder, hypotonia, and hepatopathy|not provided
β˜…β˜…β˜†β˜†2024β†’ Residue 71
NM_002161.6(IARS1):c.1382_1383del (p.Arg461fs)Pathogenic
not provided
β˜…β˜…β˜†β˜†2024β†’ Residue 461
NM_002161.6(IARS1):c.833+1G>ALikely pathogenic
not provided
β˜…β˜†β˜†β˜†2025
NM_002161.6(IARS1):c.2512C>T (p.Arg838Ter)Likely pathogenic
Growth retardation, intellectual developmental disorder, hypotonia, and hepatopathy
β˜…β˜†β˜†β˜†2025β†’ Residue 838
NM_002161.6(IARS1):c.2137+1G>CLikely pathogenic
not provided
β˜…β˜†β˜†β˜†2025
NM_002161.6(IARS1):c.1658C>A (p.Pro553His)Likely pathogenic
Growth retardation, intellectual developmental disorder, hypotonia, and hepatopathy
β˜…β˜†β˜†β˜†2025β†’ Residue 553
NM_002161.6(IARS1):c.423G>A (p.Trp141Ter)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 141
NM_002161.6(IARS1):c.128_153dup (p.Gly52fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 52
NM_002161.6(IARS1):c.276+1G>ALikely pathogenic
not provided
β˜…β˜†β˜†β˜†2025
NM_002161.6(IARS1):c.3410-2A>GLikely pathogenic
not provided
β˜…β˜†β˜†β˜†2025
NM_002161.6(IARS1):c.2430-2A>GLikely pathogenic
not provided
β˜…β˜†β˜†β˜†2025
NM_002161.6(IARS1):c.2939C>G (p.Ser980Ter)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 980
NM_002161.6(IARS1):c.26_27del (p.Ile9fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2025β†’ Residue 9
NM_002161.6(IARS1):c.1252C>T (p.Arg418Ter)Pathogenic
Growth retardation, intellectual developmental disorder, hypotonia, and hepatopathy
β˜…β˜†β˜†β˜†2024β†’ Residue 418
NM_002161.6(IARS1):c.1156C>T (p.Arg386Ter)Pathogenic
not provided
β˜…β˜†β˜†β˜†2024β†’ Residue 386
NM_002161.6(IARS1):c.773dup (p.Leu258fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2024β†’ Residue 258
NM_002161.6(IARS1):c.2108_2109del (p.Leu703fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2023β†’ Residue 703
NM_002161.6(IARS1):c.1043_1044del (p.Pro348fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2023β†’ Residue 348
View on ClinVar β†—
Related Genes
CARS1Protein interaction100%GARS1Protein interaction100%HARS1Protein interaction100%KARS1Protein interaction100%MARS1Protein interaction100%QARS1Protein interaction100%
Tissue Expression6 tissues
Heart
100%
Brain
90%
Lung
70%
Liver
60%
Ovary
58%
Bone Marrow
54%
Gene Interaction Network
Click a node to explore
IARS1CARS1GARS1HARS1KARS1MARS1QARS1
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted Β· UniProt P41252
View on AlphaFold β†—
Constraintβ“˜
LOEUFβ“˜
0.91LoF Tolerant
pLIβ“˜
0.00Tolerant
Observed/Expected LoF0.75 [0.61–0.91]
RankingsWhere IARS1 stands among ~20K protein-coding genes
  • #1,522of 20,598
    Most Researched252 Β· top 10%
  • #1,609of 5,498
    Most Pathogenic Variants37
  • #8,307of 17,882
    Most Constrained (LOEUF)0.91
Genes detectedIARS1
Sources retrieved11 papers
Response timeβ€”
πŸ“„ Sources
11β–Ό
1
Atypical Presentation of
PMID: 40365325
JIMD Rep Β· 2025
1.00
2
Mechanisms and Future Research Perspectives on Mitochondrial Diseases Associated with Isoleucyl-tRNA Synthetase Gene Mutations.
PMID: 39062673
Genes (Basel) Β· 2024
1.00
3
Molecular and Pathological Analyses of IARS1-Deficient Mice: An IARS Disorder Model.
PMID: 37108118
Int J Mol Sci Β· 2023
0.90
4
Isoleucine-to-valine substitutions support cellular physiology during isoleucine deprivation.
PMID: 39657787
Nucleic Acids Res Β· 2025
0.80
5
Isoleucyl-tRNA synthetase 1 is essential for embryogenesis in mice.
PMID: 41192854
J Vet Med Sci Β· 2026
0.70