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10 sources retrieved · Most recent: April 2026 · Index updated 14 days ago
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KCND1
potassium voltage-gated channel subfamily D member 1
Chromosome X · Xp11.23
NCBI Gene: 3750Ensembl: ENSG00000102057.12HGNC: HGNC:6237UniProt: Q9NSA2
21PubMed Papers
20Diseases
7Drugs
0Pathogenic Variants
FUNCTIONAL ROLE
Ion ChannelTransporter
CLINICAL
FDA Approved Target
DATA QUALITY
✓ Experimental GO Evidence✓ Swiss-Prot Reviewed
A-type (transient outward) potassium channel activityneuronal cell bodydendritic spinepostsynaptic membranemultiple sclerosisMyasthenia gravisLambert-Eaton myasthenic syndromeMuscle weakness
✦AI Summary

KCND1 encodes Kv4.1, an A-type voltage-gated potassium channel subunit that plays critical roles in neuronal excitability and development 1. The channel mediates rapidly inactivating A-type currents in neurons and exhibits low-threshold properties with voltage-dependent recovery kinetics 2. KCND1 is widely expressed in human brain, heart, liver, kidney, thyroid, and pancreas tissues 2. Functionally, Kv4.1 channels contribute to regulation of repetitive firing rates in suprachiasmatic nucleus neurons and may influence circadian rhythms, with auxiliary subunits like KCNIP1 and DPP10 modulating channel kinetics [UniProt summary]. Pathogenic variants in KCND1 cause an X-linked neurodevelopmental disorder characterized by developmental delays, neuropsychiatric symptoms, and epilepsy in affected males, while carrier mothers remain unaffected 1. The variants affect diverse channel properties and occur throughout the protein structure, including cytoplasmic domains and transmembrane segments 1. Additionally, KCND1 variants have been identified as potential contributors to nonobstructive azoospermia 3 and pediatric epilepsy 4, suggesting broader roles in male fertility and seizure disorders.

Sources cited
1
KCND1 variants cause X-linked neurodevelopmental disorder with developmental delays and epilepsy
PMID: 38772379
2
KCND1 encodes Kv4.1 A-type potassium channel and has broad tissue expression
PMID: 10729221
3
KCND1 variants identified as potential contributors to nonobstructive azoospermia
PMID: 36017582
4
KCND1 variant detected as candidate gene in pediatric epilepsy
PMID: 30182498
⚠Limited data available — This gene has 4 indexed publications. Summary and analysis may be incomplete.
Disease Associationsⓘ20
multiple sclerosisOpen Targets
0.59Moderate
Myasthenia gravisOpen Targets
0.56Moderate
Lambert-Eaton myasthenic syndromeOpen Targets
0.55Moderate
Muscle weaknessOpen Targets
0.46Moderate
congenital myasthenic syndromeOpen Targets
0.43Moderate
Congenital myasthenic syndromesOpen Targets
0.43Moderate
neoplasmOpen Targets
0.37Weak
cancerOpen Targets
0.37Weak
neurodegenerative diseaseOpen Targets
0.37Weak
autoimmune diseaseOpen Targets
0.37Weak
autoimmune disorder of the nervous systemOpen Targets
0.37Weak
cardiac arrhythmiaOpen Targets
0.37Weak
immune system diseaseOpen Targets
0.37Weak
Increased muscle fatiguabilityOpen Targets
0.37Weak
nervous system diseaseOpen Targets
0.37Weak
nervous system neoplasmOpen Targets
0.37Weak
neuromuscular diseaseOpen Targets
0.37Weak
neuromuscular junction diseaseOpen Targets
0.37Weak
paraneoplastic neurologic syndromeOpen Targets
0.37Weak
small cell carcinomaOpen Targets
0.37Weak
Pathogenic Variants
No pathogenic variants reported on ClinVar for this gene.
View on ClinVar ↗
Drug Targets7
AMIFAMPRIDINEApproved
Voltage-gated potassium channel blocker
Myasthenia gravis
AMIFAMPRIDINE PHOSPHATEApproved
Voltage-gated potassium channel blocker
Lambert-Eaton myasthenic syndrome
DALFAMPRIDINEApproved
Voltage-gated potassium channel blocker
multiple sclerosis
GUANIDINEPhase III
Voltage-gated potassium channel blocker
neuroendocrine neoplasm
GUANIDINE HYDROCHLORIDEApproved
Voltage-gated potassium channel blocker
Myasthenia gravis
NERISPIRDINEPhase II
Voltage-gated potassium channel blocker
multiple sclerosis
TEDISAMILApproved
Voltage-gated potassium channel blocker
cardiac arrhythmia
Related Genes
KCNA3Shared pathway100%KCNA6Shared pathway100%KCNA7Shared pathway100%KCNA10Shared pathway100%KCNV2Shared pathway100%KCNV1Shared pathway100%
Tissue Expression6 tissues
Bone Marrow
100%
Ovary
55%
Lung
49%
Brain
32%
Liver
30%
Heart
14%
Gene Interaction Network
Click a node to explore
KCND1KCNA3KCNA6KCNA7KCNA10KCNV2KCNV1
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted · UniProt Q9NSA2
View on AlphaFold ↗
RankingsWhere KCND1 stands among ~20K protein-coding genes
  • #13,938of 20,598
    Most Researched21
  • #334of 1,025
    FDA-Approved Drug Targets5
Genes detectedKCND1
Sources retrieved10 papers
Response time—
📄 Sources
10▼
1
Whole-genome sequencing identifies new candidate genes for nonobstructive azoospermia.
PMID: 36017582
Andrology · 2022
1.00
2
X Chromosome Contribution to the Genetic Architecture of Primary Biliary Cholangitis.
PMID: 33675743
Gastroenterology · 2021
0.90
3
Etiological involvement of KCND1 variants in an X-linked neurodevelopmental disorder with variable expressivity.
PMID: 38772379
Am J Hum Genet · 2024
0.80
4
Gene structures and expression profiles of three human KCND (Kv4) potassium channels mediating A-type currents I(TO) and I(SA).
PMID: 10729221
Genomics · 2000
0.70
5
Circular RNA mmu_circ_0005019 inhibits fibrosis of cardiac fibroblasts and reverses electrical remodeling of cardiomyocytes.
PMID: 34154526
BMC Cardiovasc Disord · 2021
0.60