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GeneE
10 sources retrieved Β· Most recent: April 2026 Β· Index updated 14 days ago
β“˜GeneE is for informational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment.
RHOBTB2
Rho related BTB domain containing 2
Chromosome 8 Β· 8p21.3
NCBI Gene: 23221Ensembl: ENSG00000008853.19HGNC: HGNC:18756UniProt: Q9BYZ6
53PubMed Papers
21Diseases
0Drugs
15Pathogenic Variants
CLINICAL
OMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
ubiquitin-like ligase-substrate adaptor activityubiquitin-dependent protein catabolic processCul3-RING ubiquitin ligase complexprotein bindinggenetic developmental and epileptic encephalopathySeizuregenetic disorderbasal cell carcinoma
✦AI Summary

RHOBTB2 is an atypical Rho-family GTPase that functions as a substrate adapter protein in CUL3-based ubiquitin ligase complexes, regulating protein degradation and cellular processes 1. The protein contains both a GTPase domain and a BTB domain, with distinct functional consequences depending on variant location 2. RHOBTB2 serves as a tumor suppressor in breast cancer, where it inhibits cell migration and invasion through upregulation of BRMS1 and downregulation of ezrin phosphorylation 3. The gene is frequently silenced by promoter hypermethylation in breast cancers, particularly those that are progesterone receptor-negative 4. RHOBTB2 is also a direct target of E2F1 transcription factor and plays roles in cell cycle progression and apoptosis, with expression upregulated during mitosis and drug-induced apoptosis 5. In acute myeloid leukemia, RHOBTB2 promotes cell proliferation by stabilizing KLHL13 protein and modulating Hippo-YAP1 signaling 6. Pathogenic variants cause developmental and epileptic encephalopathy, with missense variants in the BTB domain causing severe early-onset seizures, while GTPase domain variants produce more variable neurodevelopmental phenotypes 2. The epileptic phenotype involves deregulated ion channels and altered neuronal excitability 7.

Sources cited
1
Functions as substrate adapter in CUL3-based ubiquitin ligase complexes
PMID: 27941885
2
BTB and GTPase domains have distinct functional consequences for disease phenotypes
PMID: 37165955
3
Acts as tumor suppressor inhibiting breast cancer cell migration and invasion
PMID: 20930524
4
Frequently silenced by promoter hypermethylation in breast cancer
PMID: 24356943
5
Direct target of E2F1 with roles in cell cycle and apoptosis
PMID: 18039672
6
Promotes AML cell proliferation through KLHL13 stabilization and Hippo-YAP1 signaling
PMID: 41107424
7
Pathogenic variants cause epilepsy through deregulated ion channels and altered neuronal excitability
PMID: 39849855
Disease Associationsβ“˜21
genetic developmental and epileptic encephalopathyOpen Targets
0.68Moderate
SeizureOpen Targets
0.52Moderate
genetic disorderOpen Targets
0.50Moderate
basal cell carcinomaOpen Targets
0.47Moderate
developmental and epileptic encephalopathyOpen Targets
0.46Moderate
complex neurodevelopmental disorderOpen Targets
0.46Moderate
renal carcinomaOpen Targets
0.42Moderate
clear cell renal carcinomaOpen Targets
0.41Moderate
Global developmental delayOpen Targets
0.37Weak
Intellectual disabilityOpen Targets
0.37Weak
alternating hemiplegia of childhoodOpen Targets
0.37Weak
early-infantile DEEOpen Targets
0.37Weak
Secondary microcephalyOpen Targets
0.37Weak
renal cell carcinomaOpen Targets
0.34Weak
choreaOpen Targets
0.33Weak
DystoniaOpen Targets
0.33Weak
dystonic disorderOpen Targets
0.33Weak
prostate carcinomaOpen Targets
0.32Weak
Rett syndromeOpen Targets
0.27Weak
bacterial diseaseOpen Targets
0.13Weak
Developmental and epileptic encephalopathy 64UniProt
Pathogenic Variants15
NM_015178.3(RHOBTB2):c.280C>T (p.Arg94Cys)Likely pathogenic
not provided|Developmental and epileptic encephalopathy, 64
β˜…β˜…β˜†β˜†2026β†’ Residue 94
NM_015178.3(RHOBTB2):c.1466G>A (p.Arg489Gln)Pathogenic
Developmental and epileptic encephalopathy, 64|Dystonic disorder;Chorea|Inborn genetic diseases|not provided
β˜…β˜…β˜†β˜†2025β†’ Residue 489
NM_015178.3(RHOBTB2):c.1465C>T (p.Arg489Trp)Pathogenic
Rett syndrome|Developmental and epileptic encephalopathy, 64|not provided|Inborn genetic diseases|Seizure
β˜…β˜…β˜†β˜†2025β†’ Residue 489
NM_015178.3(RHOBTB2):c.1453C>T (p.Arg485Cys)Pathogenic
Developmental and epileptic encephalopathy, 64|not provided
β˜…β˜…β˜†β˜†2025β†’ Residue 485
NM_015178.3(RHOBTB2):c.1382G>A (p.Arg461His)Pathogenic
Developmental and epileptic encephalopathy, 64|not provided|Inborn genetic diseases|Seizure
β˜…β˜…β˜†β˜†2025β†’ Residue 461
NM_015178.3(RHOBTB2):c.1462A>G (p.Asn488Asp)Pathogenic
Inborn genetic diseases|Developmental and epileptic encephalopathy, 64|not provided
β˜…β˜…β˜†β˜†2024β†’ Residue 488
NM_015178.3(RHOBTB2):c.1465C>G (p.Arg489Gly)Pathogenic
not provided|Developmental and epileptic encephalopathy, 64
β˜…β˜…β˜†β˜†2021β†’ Residue 489
NM_015178.3(RHOBTB2):c.656C>T (p.Ser219Phe)Likely pathogenic
Developmental and epileptic encephalopathy, 64
β˜…β˜†β˜†β˜†2025β†’ Residue 219
NM_015178.3(RHOBTB2):c.1113dup (p.Arg372fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2024β†’ Residue 372
NM_015178.3(RHOBTB2):c.394C>T (p.Arg132Ter)Likely pathogenic
Developmental and epileptic encephalopathy, 64
β˜…β˜†β˜†β˜†2024β†’ Residue 132
NM_015178.3(RHOBTB2):c.293G>A (p.Gly98Glu)Pathogenic
not provided|RHOBTB2-related disorder
β˜…β˜†β˜†β˜†2023β†’ Residue 98
NM_015178.3(RHOBTB2):c.268C>T (p.His90Tyr)Likely pathogenic
See cases
β˜…β˜†β˜†β˜†2022β†’ Residue 90
NM_015178.3(RHOBTB2):c.1411G>A (p.Glu471Lys)Pathogenic
not provided
β˜…β˜†β˜†β˜†2020β†’ Residue 471
NM_015178.3(RHOBTB2):c.1355C>G (p.Ala452Gly)Likely pathogenic
Developmental and epileptic encephalopathy, 64
β˜…β˜†β˜†β˜†2018β†’ Residue 452
NM_015178.3(RHOBTB2):c.103G>T (p.Ala35Ser)Likely pathogenic
Developmental and epileptic encephalopathy, 64
β˜…β˜†β˜†β˜†β†’ Residue 35
View on ClinVar β†—
Related Genes
KLHL13Protein interaction100%KLHL9Protein interaction100%CUL3Protein interaction97%KEAP1Protein interaction97%RHOBTB1Protein interaction93%MSI2Protein interaction71%
Tissue Expression6 tissues
Lung
100%
Heart
59%
Brain
41%
Ovary
32%
Bone Marrow
8%
Liver
6%
Gene Interaction Network
Click a node to explore
RHOBTB2KLHL13KLHL9CUL3KEAP1RHOBTB1MSI2
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted Β· UniProt Q9BYZ6
View on AlphaFold β†—
Constraintβ“˜
LOEUFβ“˜
0.76LoF Tolerant
pLIβ“˜
0.00Tolerant
Observed/Expected LoF0.57 [0.44–0.76]
RankingsWhere RHOBTB2 stands among ~20K protein-coding genes
  • #8,483of 20,598
    Most Researched53
  • #2,462of 5,498
    Most Pathogenic Variants15
  • #6,107of 17,882
    Most Constrained (LOEUF)0.76
Genes detectedRHOBTB2
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
[Neurodevelopmental impact of a mutation in the RHOBTB2 gene].
PMID: 39129541
Rev Med Liege Β· 2024
1.00
2
Ectopic expression of RhoBTB2 inhibits migration and invasion of human breast cancer cells.
PMID: 20930524
Cancer Biol Ther Β· 2010
0.90
3
RHOBTB2 enhances cell proliferation of acute myeloid leukemia by modulating Hippo-YAP1 signaling and dependent of KLHL13.
PMID: 41107424
Sci Rep Β· 2025
0.80
4
Genotype-phenotype correlations in RHOBTB2-associated neurodevelopmental disorders.
PMID: 37165955
Genet Med Β· 2023
0.70
5
Deregulated ion channels contribute to RHOBTB2-associated developmental and epileptic encephalopathy.
PMID: 39849855
Hum Mol Genet Β· 2025
0.60