HomeAboutRankingsData Sources
Β© 2026 GeneE
🧬
GeneE
10 sources retrieved Β· Most recent: April 2026 Β· Index updated 15 days ago
β“˜GeneE is for informational purposes only. It is not a substitute for professional medical advice, diagnosis, or treatment.
NDUFAF1
NADH:ubiquinone oxidoreductase complex assembly factor 1
Chromosome 15 Β· 15q15.1
NCBI Gene: 51103Ensembl: ENSG00000137806.11HGNC: HGNC:18828UniProt: Q9Y375
48PubMed Papers
21Diseases
3Drugs
4Pathogenic Variants
FUNCTIONAL ROLE
Hub Gene
CLINICAL
FDA Approved TargetOMIM Disease Gene
DATA QUALITY
βœ“ Experimental GO Evidenceβœ“ Swiss-Prot Reviewed
protein bindingmitochondrial respiratory chain complex I assemblymitochondrionmitochondrial complex I intermediate assembly complexmitochondrial complex I deficiencymitochondrial complex I deficiency, nuclear type 11type 2 diabetes mellitusdiabetes mellitus
✦AI Summary

NDUFAF1 (NADH:ubiquinone oxidoreductase complex assembly factor 1) is a mitochondrial assembly factor essential for respiratory complex I biogenesis. As a component of the MCIA complex, NDUFAF1 mediates the nucleation and maturation of complex I, the largest multiprotein enzyme in oxidative phosphorylation 1. Structurally, NDUFAF1 forms a core assembly complex with ACAD9 and ECSIT, locking the central ND3 subunit in an assembly-competent conformation and facilitating sequential incorporation of the 12-subunit proximal proton pump module 23. NDUFAF1 knockdown reduces complex I amount and activity, impairing mitochondrial respiration and increasing glycolytic flux 14. Biallelic NDUFAF1 mutations cause mitochondrial complex I deficiency, nuclear type 11, a severe metabolic disorder with heterogeneous clinical presentations. Disease manifestations include pediatric hypertrophic cardiomyopathy, leukodystrophy with white matter lesions, developmental regression, and peripheral neuropathy 56. Beyond genetic causes, NDUFAF1 expression is downregulated in childhood allergic asthma and K-Ras-induced mitochondrial dysfunction, suggesting its role extends to disease-associated metabolic alterations 74. Clinically, NDUFAF1 and related mitochondrial genes represent emerging biomarkers for metabolic and genetic diseases affecting energy metabolism.

Sources cited
1
NDUFAF1 is a mitochondrial assembly protein involved in complex I assembly; knockdown reduces complex I amount and activity
PMID: 16218961
2
NDUFAF1 forms core assembly complex with NDUFAC2 and CIA84; locks ND3 subunit in assembly-competent conformation for complex I maturation
PMID: 36383672
3
NDUFAF1 interacts with ACAD9 and ECSIT to form stable ternary complex essential for complex I assembly
PMID: 34646991
4
Biallelic NDUFAF1 variants cause mitochondrial complex I deficiency, nuclear type 11, presenting as pediatric hypertrophic cardiomyopathy
PMID: 39821332
5
NDUFAF1 mutations cause leukodystrophy with white matter lesions and developmental regression due to complex I deficiency
PMID: 24963768
6
NDUFAF1 is downregulated in childhood allergic asthma and identified as mitochondrial-related biomarker
PMID: 38783263
7
NDUFAF1 expression decreases significantly in K-Ras-induced mitochondrial dysfunction; knockdown causes respiration deficiency and increased glycolysis
PMID: 25714130
Disease Associationsβ“˜21
mitochondrial complex I deficiencyOpen Targets
0.73Strong
mitochondrial complex I deficiency, nuclear type 11Open Targets
0.65Moderate
type 2 diabetes mellitusOpen Targets
0.61Moderate
diabetes mellitusOpen Targets
0.60Moderate
mitochondrial complex I deficiency, nuclear type 1Open Targets
0.55Moderate
mitochondrial diseaseOpen Targets
0.55Moderate
neurodegenerative diseaseOpen Targets
0.54Moderate
polycystic ovary syndromeOpen Targets
0.41Moderate
gestational diabetesOpen Targets
0.41Moderate
Insulin resistanceOpen Targets
0.40Moderate
obesityOpen Targets
0.40Weak
prediabetes syndromeOpen Targets
0.40Weak
metabolic syndromeOpen Targets
0.39Weak
type 1 diabetes mellitusOpen Targets
0.39Weak
Disorder of lipid metabolismOpen Targets
0.38Weak
agingOpen Targets
0.37Weak
COVID-19Open Targets
0.37Weak
benign neoplasm of eyeOpen Targets
0.36Weak
prostate cancerOpen Targets
0.36Weak
abnormal glucose toleranceOpen Targets
0.36Weak
Mitochondrial complex I deficiency, nuclear type 11UniProt
Pathogenic Variants4
NM_016013.4(NDUFAF1):c.532del (p.Thr178fs)Pathogenic
not provided
β˜…β˜†β˜†β˜†2015β†’ Residue 178
NM_016013.4(NDUFAF1):c.2T>C (p.Met1Thr)Pathogenic
not provided
β˜…β˜†β˜†β˜†2014β†’ Residue 1
NM_016013.4(NDUFAF1):c.650G>A (p.Arg217Gln)Likely pathogenic
not provided
β˜…β˜†β˜†β˜†2013β†’ Residue 217
NM_016013.4(NDUFAF1):c.619A>C (p.Thr207Pro)Pathogenic
Mitochondrial complex I deficiency, nuclear type 11
β˜†β˜†β˜†β˜†2007β†’ Residue 207
View on ClinVar β†—
Drug Targets3
ME-344Phase I/II
Mitochondrial complex I (NADH dehydrogenase) inhibitor
breast cancer
METFORMINApproved
Mitochondrial complex I (NADH dehydrogenase) inhibitor
diabetes mellitus
METFORMIN HYDROCHLORIDEApproved
Mitochondrial complex I (NADH dehydrogenase) inhibitor
type 2 diabetes mellitus
Related Genes
NDUFAB1Protein interaction100%NDUFV2Protein interaction100%NDUFA9Protein interaction100%NDUFA5Protein interaction100%NDUFB8Protein interaction100%NDUFB11Protein interaction100%
Tissue Expression6 tissues
Heart
100%
Brain
98%
Liver
87%
Ovary
37%
Lung
36%
Bone Marrow
12%
Gene Interaction Network
Click a node to explore
NDUFAF1NDUFAB1NDUFV2NDUFA9NDUFA5NDUFB8NDUFB11
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted Β· UniProt Q9Y375
View on AlphaFold β†—
Constraintβ“˜
LOEUFβ“˜
0.84LoF Tolerant
pLIβ“˜
0.01Tolerant
Observed/Expected LoF0.54 [0.35–0.84]
RankingsWhere NDUFAF1 stands among ~20K protein-coding genes
  • #9,103of 20,598
    Most Researched48
  • #666of 1,025
    FDA-Approved Drug Targets2
  • #3,798of 5,498
    Most Pathogenic Variants4
  • #7,244of 17,882
    Most Constrained (LOEUF)0.84
Genes detectedNDUFAF1
Sources retrieved10 papers
Response timeβ€”
πŸ“„ Sources
10β–Ό
1
Identification of mitochondria-related biomarkers in childhood allergic asthma.
PMID: 38783263
BMC Med Genomics Β· 2024
1.00
2
Human mitochondrial complex I assembly is mediated by NDUFAF1.
PMID: 16218961
FEBS J Β· 2005
0.90
3
Mitochondrial Complex I Deficiency: Unraveling the Relevance of NDUFAF1 in Pediatric Hypertrophic Cardiomyopathy.
PMID: 39821332
Am J Med Genet A Β· 2025
0.80
4
Insights into complex I assembly: Function of NDUFAF1 and a link with cardiolipin remodeling.
PMID: 36383672
Sci Adv Β· 2022
0.70
5
Identification of NDUFAF1 in mediating K-Ras induced mitochondrial dysfunction by a proteomic screening approach.
PMID: 25714130
Oncotarget Β· 2015
0.60