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8 sources retrieved · Most recent: April 2026 · Index updated 14 days ago
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FAM135A
family with sequence similarity 135 member A
Chromosome 6 · 6q13
NCBI Gene: 57579Ensembl: ENSG00000082269.17HGNC: HGNC:21084UniProt: D6RCC7
38PubMed Papers
20Diseases
0Drugs
0Pathogenic Variants
DATA QUALITY
✓ Experimental GO Evidence✓ Swiss-Prot Reviewed
lipid metabolic processbile duct disorderintracranial hemorrhagecellulitisskin infection
✦AI Summary

FAM135A (Family with Sequence Similarity 135 Member A) is a gene located on chromosome 6 with roles in cancer progression and immune regulation. Primary function: FAM135A is implicated in perineural invasion in prostate cancer, where GRPR-induced FAM135A expression promotes tumor-nerve interaction through nuclear translocation mediated by RAN protein 1. The gene functions as a transcriptional regulator, with TENM3 identified as a direct transcriptional target 1. Mechanism: FAM135A exhibits nuclear enrichment and regulates downstream pathways involved in cancer cell invasion and neural interaction 1. In breast cancer, FAM135A acts as a miRNA target within the MIR17HG/miR-454-3p regulatory network, where high FAM135A expression correlates with better prognosis and reduced proliferation 2. Gene expression: FAM135A shows differential regulation across disease contexts—it is inhibited during CVB3 viral infection 3 and exhibits antagonistic expression patterns in rheumatoid arthritis and systemic lupus erythematosus 4. Disease relevance: Beyond prostate and breast cancers, FAM135A variants have been identified as candidate susceptibility loci for Alzheimer's disease in East Asian populations 5 and show mutations in pancreatic neuroendocrine tumors 6. Clinical significance: FAM135A serves as a potential biomarker and therapeutic target for prostate cancer perineural invasion and chemotherapy resistance in oral cancers 7, positioning it as a multi-disease relevant gene warranting further investigation.

Sources cited
1
FAM135A is a GRPR-induced oncodriver in prostate cancer that promotes perineural invasion through nuclear translocation and TENM3 transcriptional regulation
PMID: 41250119
2
FAM135A expression is inhibited during CVB3 viral infection in HeLa cells and is regulated by miRNA networks
PMID: 31784561
3
FAM135A is downregulated in oral cancer cells with limited chemotherapy resistance and may influence chemosensitivity
PMID: 38396844
4
FAM135A exhibits antagonistic expression patterns between rheumatoid arthritis and systemic lupus erythematosus
PMID: 36928613
5
FAM135A (Fam135a in mice) was identified as a candidate gene in a chromosomal locus modulating ethanol-anxiety interactions
PMID: 25991709
6
FAM135A harbors mutations common across pancreatic neuroendocrine tumor cell lines
PMID: 35394261
7
FAM135A is a miRNA target of miR-454-3p in the MIR17HG ceRNA network; high FAM135A expression correlates with better breast cancer prognosis and reduced proliferation
PMID: 36943627
8
FAM135A is identified as a candidate susceptibility locus for Alzheimer's disease or cognition in East Asian populations
PMID: 41700061
Disease Associationsⓘ20
bile duct disorderOpen Targets
0.30Weak
intracranial hemorrhageOpen Targets
0.28Weak
cellulitisOpen Targets
0.27Weak
skin infectionOpen Targets
0.27Weak
Abnormality of the gastrointestinal tractOpen Targets
0.27Weak
mucositisOpen Targets
0.18Weak
stomatitisOpen Targets
0.18Weak
spinal fractureOpen Targets
0.18Weak
neoplasmOpen Targets
0.08Suggestive
prostate cancerOpen Targets
0.07Suggestive
breast cancerOpen Targets
0.06Suggestive
Familial exudative vitreoretinopathyOpen Targets
0.05Suggestive
hemoglobin D diseaseOpen Targets
0.04Suggestive
retinitis pigmentosaOpen Targets
0.04Suggestive
exfoliation syndromeOpen Targets
0.04Suggestive
hemolytic anemia due to glutathione reductase deficiencyOpen Targets
0.04Suggestive
posterior cortical atrophyOpen Targets
0.04Suggestive
Familial ocular anterior segment mesenchymal dysgenesisOpen Targets
0.03Suggestive
hemoglobin E diseaseOpen Targets
0.03Suggestive
snowflake vitreoretinal degenerationOpen Targets
0.03Suggestive
Pathogenic Variants
No pathogenic variants reported on ClinVar for this gene.
View on ClinVar ↗
Related Genes
ZNF202Shared pathway100%FAM135BShared pathway100%PLCXD1Shared pathway100%PLCXD3Shared pathway100%PLCXD2Shared pathway100%GDPD4Shared pathway100%
Tissue Expression6 tissues
Heart
100%
Brain
85%
Ovary
83%
Bone Marrow
50%
Lung
50%
Liver
39%
Gene Interaction Network
Click a node to explore
FAM135AZNF202FAM135BPLCXD1PLCXD3PLCXD2GDPD4
PROTEIN STRUCTURE
Preparing viewer…
AlphaFoldAI-predicted · UniProt Q9P2D6
View on AlphaFold ↗
Constraintⓘ
LOEUFⓘ
0.69LoF Tolerant
pLIⓘ
0.00Tolerant
Observed/Expected LoF0.56 [0.46–0.69]
RankingsWhere FAM135A stands among ~20K protein-coding genes
  • #10,471of 20,598
    Most Researched38
  • #5,221of 17,882
    Most Constrained (LOEUF)0.69
Genes detectedFAM135A
Sources retrieved8 papers
Response time—
📄 Sources
8▼
1
GRPR-induced FAM135A expression promote perineural invasion in prostate cancer.
PMID: 41250119
Mol Cancer · 2025
1.00
2
Construction of miRNA-target networks using microRNA profiles of CVB3-infected HeLa cells.
PMID: 31784561
Sci Rep · 2019
0.88
3
Differential Expression of MicroRNA MiR-145 and MiR-155 Downstream Targets in Oral Cancers Exhibiting Limited Chemotherapy Resistance.
PMID: 38396844
Int J Mol Sci · 2024
0.75
4
Deciphering novel common gene signatures for rheumatoid arthritis and systemic lupus erythematosus by integrative analysis of transcriptomic profiles.
PMID: 36928613
PLoS One · 2023
0.63
5
Identification of candidate genes that underlie the QTL on chromosome 1 that mediates genetic differences in stress-ethanol interactions.
PMID: 25991709
Physiol Genomics · 2015
0.50