M6PR (mannose-6-phosphate receptor, cation-dependent) functions as a cargo receptor mediating transport of phosphorylated lysosomal enzymes from the Golgi complex and cell surface to lysosomes. 1 Lysosomal enzymes bearing phosphomannosyl residues bind specifically to M6PR in the Golgi apparatus; the resulting receptor-ligand complex is transported to acidic prelysosomal compartments where low pH mediates complex dissociation. M6PR operates through clathrin-coated endocytic vesicles and the retromer complex, with recent studies revealing that retromer-mediated recycling of M6PR to the plasma membrane represents a key regulatory mechanism. 2 M6PR dysfunction has significant disease relevance. CLN3 mutations in Batten disease cause M6PR mis-trafficking, leading to mis-sorting of lysosomal enzymes and defective autophagic-lysosomal reformation. 1 Additionally, M6P biosynthesis deficiency impairs M6PR ligand availability, reducing lysosomal enzyme targeting efficiency. 2 Clinically, M6PR has emerged as a therapeutic target. Lysosome-targeting chimeras (LYTACs) exploit M6PR to direct extracellular proteins for lysosomal degradation, representing a novel degradation platform complementary to traditional inhibitory approaches. 3 LYTACs successfully degrade therapeutically relevant proteins including VEGF, EGFR, and PD-L1 in various disease models. 4 This strategy offers advantages for targeting proteins with inaccessible activity profiles and extends therapeutic reach beyond cytosolic targets.
No related genes found for this gene.
No tissue expression data available for this gene.